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Plos One
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March 19, 2024
Feasibility and utility of in-home body weight support harness system use in young children treated for spinal muscular atrophy: A single-arm prospective cohort study
Megan A Iammarino, Lindsay N Alfano, Natalie F Reash, et al.
Developmental Medicine and Child Neurology
|
December 19, 2024
Psychometric evaluation of the PROMIS parent proxy mobility item bank for use in Duchenne muscular dystrophy
Linda Pax Lowes, Corinne M Le Reun, Lindsay N Alfano, et al.
Frontiers in Neurology
|
June 10, 2025
Psychometric analysis of the patient-reported outcomes measurement information system parent proxy physical function-upper extremity item bank for children with Duchenne muscular dystrophy
Linda Pax Lowes, Corinne M Le Reun, Teofil Ciobanu, et al.
Journal of Neuromuscular Diseases
|
May 13, 2025
A prospective observational study assessing the functional disease progression of LGMDR4, betasarcoglycan-related limb girdle muscular dystrophy
Megan A Iammarino, Natalie F Reash, Kiana Shannon, et al.
Plos One
|
May 16, 2024
Validity of remote live stream video evaluation of the North Star Ambulatory Assessment in patients with Duchenne muscular dystrophy
Linda P Lowes, Lindsay N Alfano, Megan A Iammarino, et al.
Muscle & Nerve
|
June 4, 2026
Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study
Jerry R Mendell, Zarife Sahenk, Linda P Lowes, et al.
Developmental Medicine and Child Neurology
|
April 10, 2019
ACTIVE (Ability Captured Through Interactive Video Evaluation) workspace volume video game to quantify meaningful change in spinal muscular atrophy
Lindsay N Alfano, Natalie F Miller, Megan A Iammarino, et al.
Eclinicalmedicine
|
April 22, 2026
Safety and efficacy of droxidopa for dysautonomia in adults with Menkes disease and occipital horn syndrome in the USA: a randomised phase 1/2a crossover trial
Maryann M Kaler, Guy Brock, Christopher J Jeanty, et al.
Pediatric Neurology
|
September 26, 2020
Natural History of Steroid-Treated Young Boys With Duchenne Muscular Dystrophy Using the NSAA, 100m, and Timed Functional Tests
Natalie F Miller, Lindsay N Alfano, Megan A Iammarino, et al.
JAMA Neurology
|
May 17, 2021
Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy
Jerry R Mendell, Samiah A Al-Zaidy, Kelly J Lehman, et al.
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Search research articles
Search
Showing results (1-10 of 25) with videos related to
Sort By:
Page
of 3
Plos One
|
March 19, 2024
Feasibility and utility of in-home body weight support harness system use in young children treated for spinal muscular atrophy: A single-arm prospective cohort study
Megan A Iammarino, Lindsay N Alfano, Natalie F Reash, et al.
Developmental Medicine and Child Neurology
|
December 19, 2024
Psychometric evaluation of the PROMIS parent proxy mobility item bank for use in Duchenne muscular dystrophy
Linda Pax Lowes, Corinne M Le Reun, Lindsay N Alfano, et al.
Frontiers in Neurology
|
June 10, 2025
Psychometric analysis of the patient-reported outcomes measurement information system parent proxy physical function-upper extremity item bank for children with Duchenne muscular dystrophy
Linda Pax Lowes, Corinne M Le Reun, Teofil Ciobanu, et al.
Journal of Neuromuscular Diseases
|
May 13, 2025
A prospective observational study assessing the functional disease progression of LGMDR4, betasarcoglycan-related limb girdle muscular dystrophy
Megan A Iammarino, Natalie F Reash, Kiana Shannon, et al.
Plos One
|
May 16, 2024
Validity of remote live stream video evaluation of the North Star Ambulatory Assessment in patients with Duchenne muscular dystrophy
Linda P Lowes, Lindsay N Alfano, Megan A Iammarino, et al.
Muscle & Nerve
|
June 4, 2026
Five-Year Outcomes With Delandistrogene Moxeparvovec in Patients With Duchenne Muscular Dystrophy: A Phase 1/2a Study
Jerry R Mendell, Zarife Sahenk, Linda P Lowes, et al.
Developmental Medicine and Child Neurology
|
April 10, 2019
ACTIVE (Ability Captured Through Interactive Video Evaluation) workspace volume video game to quantify meaningful change in spinal muscular atrophy
Lindsay N Alfano, Natalie F Miller, Megan A Iammarino, et al.
Eclinicalmedicine
|
April 22, 2026
Safety and efficacy of droxidopa for dysautonomia in adults with Menkes disease and occipital horn syndrome in the USA: a randomised phase 1/2a crossover trial
Maryann M Kaler, Guy Brock, Christopher J Jeanty, et al.
Pediatric Neurology
|
September 26, 2020
Natural History of Steroid-Treated Young Boys With Duchenne Muscular Dystrophy Using the NSAA, 100m, and Timed Functional Tests
Natalie F Miller, Lindsay N Alfano, Megan A Iammarino, et al.
JAMA Neurology
|
May 17, 2021
Five-Year Extension Results of the Phase 1 START Trial of Onasemnogene Abeparvovec in Spinal Muscular Atrophy
Jerry R Mendell, Samiah A Al-Zaidy, Kelly J Lehman, et al.
Page
of 3