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Clinical Genetics|November 30, 2024
WDFY3 Haploinsufficiency Is Associated With Autosomal Dominant Neurodevelopmental Disorders and MacrocephalyLudovico Graziani, Miriam Lucia Carriero, Valentina Ferradini, et al.
Molecular Syndromology|August 9, 2024
Genetic Variability of <i>SOX10</i>-Related Disorders within an Italian Family: Straddling the Line between Kallmann and Waardenburg SyndromeLudovico Graziani, Miriam Lucia Carriero, Flavio Pozzi, et al.
The Journal of Maternal-Fetal & Neonatal Medicine : the Official Journal of the European Association of Perinatal Medicine, the Federation of Asia and Oceania Perinatal Societies, the International Society of Perinatal Obstetricians|April 28, 2024
Prenatal identification of a pathogenic maternal <i>FGFR1</i> variant in two consecutive pregnancies with fetal forebrain malformationsLudovico Graziani, Sara Nuovo, Elisa Pisaneschi, et al.
Journal of Personalized Medicine|October 25, 2024
Implementing the Risk Stratification and Clinical Management of Breast Cancer Families Using Polygenic Risk Score Evaluation: A Pilot StudyBarbara Rizzacasa, Vanessa Nicolì, Chantal Tancredi, et al.
European Journal of Human Genetics : EJHG|April 26, 2020
High rate of HDR in gene editing of p.(Thr158Met) MECP2 mutational hotspotSusanna Croci, Miriam Lucia Carriero, Katia Capitani, et al.
European Journal of Human Genetics : EJHG|June 17, 2020
AAV-mediated FOXG1 gene editing in human Rett primary cellsSusanna Croci, Miriam Lucia Carriero, Katia Capitani, et al.
Journal of Personalized Medicine|July 2, 2021
Severe COVID-19 in Hospitalized Carriers of Single <i>CFTR</i> Pathogenic VariantsMargherita Baldassarri, Francesca Fava, Chiara Fallerini, et al.
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