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Progress in Neurobiology|August 6, 2011
ALS genetic modifiers that increase survival of SOD1 mice and are suitable for therapeutic developmentGiulietta Riboldi, Monica Nizzardo, Chiara Simone, et al.
Clinical Therapeutics|February 11, 2015
Therapeutic development in amyotrophic lateral sclerosisMonica Bucchia, Agnese Ramirez, Valeria Parente, et al.
Biomedicines|February 25, 2022
Targeting PTB for Glia-to-Neuron Reprogramming In Vitro and In Vivo for Therapeutic Development in Neurological DiseasesMatilde Contardo, Roberta De Gioia, Delia Gagliardi, et al.
Clinical Therapeutics|December 24, 2013
Molecular therapeutic strategies for spinal muscular atrophies: current and future clinical trialsChiara Zanetta, Monica Nizzardo, Chiara Simone, et al.
Journal of Cellular and Molecular Medicine|December 6, 2019
Spinal muscular atrophy with respiratory distress type 1: Clinical phenotypes, molecular pathogenesis and therapeutic insightsMatteo Saladini, Monica Nizzardo, Alessandra Govoni, et al.
International Journal of Molecular Sciences|January 11, 2018
Investigation of New Morpholino Oligomers to Increase Survival Motor Neuron Protein Levels in Spinal Muscular AtrophyAgnese Ramirez, Sebastiano G Crisafulli, Mafalda Rizzuti, et al.
Cellular and Molecular Life Sciences : CMLS|April 5, 2014
Stem cell transplantation for amyotrophic lateral sclerosis: therapeutic potential and perspectives on clinical translationIrene Faravelli, Giulietta Riboldi, Monica Nizzardo, et al.
Journal of Cellular and Molecular Medicine|January 10, 2014
Molecular, genetic and stem cell-mediated therapeutic strategies for spinal muscular atrophy (SMA)Chiara Zanetta, Giulietta Riboldi, Monica Nizzardo, et al.
Journal of the Neurological Sciences|September 25, 2014
The wide spectrum of clinical phenotypes of spinal muscular atrophy with respiratory distress type 1: a systematic reviewFrancesca Porro, Paola Rinchetti, Francesca Magri, et al.
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