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Cellular and Molecular Life Sciences : CMLS|March 4, 2020
Current understanding of and emerging treatment options for spinal muscular atrophy with respiratory distress type 1 (SMARD1)Martina G L Perego, Noemi Galli, Monica Nizzardo, et al.BMC Biology|March 29, 2020
TDP-43 promotes the formation of neuromuscular synapses through the regulation of Disc-large expression in Drosophila skeletal musclesNina Strah, Giulia Romano, Clelia Introna, et al.Molecular Neurobiology|August 29, 2020
Animal Models of CMT2A: State-of-art and Therapeutic ImplicationsRoberta De Gioia, Gaia Citterio, Elena Abati, et al.Molecular and Cellular Neurosciences|December 17, 2014
Pluripotent stem cell-based models of spinal muscular atrophyEmanuele Frattini, Margherita Ruggieri, Sabrina Salani, et al.Biomedicines|March 25, 2022
Stathmins and Motor Neuron Diseases: Pathophysiology and Therapeutic TargetsDelia Gagliardi, Elisa Pagliari, Megi Meneri, et al.Molecular Neurobiology|May 10, 2014
Antisense oligonucleotide therapy for the treatment of C9ORF72 ALS/FTD diseasesGiulietta Riboldi, Chiara Zanetta, Michela Ranieri, et al.International Journal of Molecular Sciences|May 2, 2020
Neural Stem Cell Transplantation for Neurodegenerative DiseasesRoberta De Gioia, Fabio Biella, Gaia Citterio, et al.Scientific Reports|May 17, 2016
Differential neuronal vulnerability identifies IGF-2 as a protective factor in ALSIlary Allodi, Laura Comley, Susanne Nichterwitz, et al.Experimental Neurology|August 25, 2019
CSF transplantation of a specific iPSC-derived neural stem cell subpopulation ameliorates the disease phenotype in a mouse model of spinal muscular atrophy with respiratory distress type 1Giulia Forotti, Monica Nizzardo, Monica Bucchia, et al.Cellular and Molecular Life Sciences : CMLS|November 19, 2011
Research advances in gene therapy approaches for the treatment of amyotrophic lateral sclerosisMonica Nizzardo, Chiara Simone, Marianna Falcone, et al.Pageof 7