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Journal of the Neurological Sciences|July 6, 2015
MFN2-related neuropathies: Clinical features, molecular pathogenesis and therapeutic perspectivesGiulia Stuppia, Federica Rizzo, Giulietta Riboldi, et al.
Human Molecular Genetics|July 24, 2010
Systemic transplantation of c-kit+ cells exerts a therapeutic effect in a model of amyotrophic lateral sclerosisStefania Corti, Monica Nizzardo, Martina Nardini, et al.
Scientific Reports|July 6, 2018
MicroRNA expression analysis identifies a subset of downregulated miRNAs in ALS motor neuron progenitorsMafalda Rizzuti, Giuseppe Filosa, Valentina Melzi, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|November 22, 2021
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical modelMargherita Bersani, Mafalda Rizzuti, Elisa Pagliari, et al.
Cellular and Molecular Life Sciences : CMLS|December 26, 2024
Targeting STMN2 for neuroprotection and neuromuscular recovery in Spinal Muscular Atrophy: evidence from in vitro and in vivo SMA modelsElisa Pagliari, Michela Taiana, Paolo Manzini, et al.
Biochimica Et Biophysica Acta|August 6, 2014
Glycogen storage disease type III: A novel Agl knockout mouse modelSerena Pagliarani, Sabrina Lucchiari, Gianna Ulzi, et al.
FASEB Journal : Official Publication of the Federation of American Societies for Experimental Biology|February 14, 2025
iPSC-derived human cortical organoids display profound alterations of cellular homeostasis following SARS-CoV-2 infection and Spike protein exposureGioia Cappelletti, Lorenzo Brambilla, Sergio Strizzi, et al.
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