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Annals of Clinical and Translational Neurology
|
April 28, 2025
Validity and Reliability of Clinical and Patient-Reported Outcomes in Multisystem Proteinopathy 1
Lindsay N Alfano, Megan A Iammarino, Natalie F Reash, et al.
Nature Medicine
|
January 4, 2024
Gene therapy with bidridistrogene xeboparvovec for limb-girdle muscular dystrophy type 2E/R4: phase 1/2 trial results
Jerry R Mendell, Eric R Pozsgai, Sarah Lewis, et al.
Muscle & Nerve
|
August 14, 2023
Long-term safety and functional outcomes of delandistrogene moxeparvovec gene therapy in patients with Duchenne muscular dystrophy: A phase 1/2a nonrandomized trial
Jerry R Mendell, Zarife Sahenk, Kelly J Lehman, et al.
Journal of Neuromuscular Diseases
|
February 20, 2025
Gross motor delays in infants and young boys with Duchenne muscular dystrophy
Linda P Lowes, Natalie F Reash, Megan A Iammarino, et al.
Muscle & Nerve
|
May 4, 2022
Comparison of strength testing modalities in dysferlinopathy
Natalie F Reash, Meredith K James, Lindsay N Alfano, et al.
Neurology. Genetics
|
November 3, 2025
Motor Function in Limb-Girdle Muscular Dystrophy R1/2A: Validation of Clinical Outcome Assessments for Clinical Care and Trial Readiness
Meredith K James, Megan A Iammarino, Natalie F Reash, et al.
Frontiers in Cell and Developmental Biology
|
July 27, 2023
Expression of SRP-9001 dystrophin and stabilization of motor function up to 2 years post-treatment with delandistrogene moxeparvovec gene therapy in individuals with Duchenne muscular dystrophy
Jerry R Mendell, Perry B Shieh, Craig M McDonald, et al.
Annals of Clinical and Translational Neurology
|
April 16, 2025
Clinical Trial Readiness in Limb Girdle Muscular Dystrophy R1 (LGMDR1): A GRASP Consortium Study
Stephanie M Hunn, Lindsay N Alfano, Aileen Jones, et al.
Annals of Clinical and Translational Neurology
|
December 15, 2024
Prospective observational study of FKRP-related limb-girdle muscular dystrophy R9: A GRASP consortium study
Lindsay N Alfano, Meredith K James, Kristine Grosfjeld Petersen, et al.
Neuromuscular Disorders : NMD
|
April 10, 2026
Natural history of limb girdle muscular dystrophy R1 (LGMDR1): a GRASP consortium study
Stephanie M Hunn, Andrew R Findlay, Lindsay N Alfano, et al.
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Search research articles
Search
Showing results (11-20 of 20) with videos related to
Sort By:
Page
of 2
You have reached the last page of results.
This site can display upto 20 results.
Annals of Clinical and Translational Neurology
|
April 28, 2025
Validity and Reliability of Clinical and Patient-Reported Outcomes in Multisystem Proteinopathy 1
Lindsay N Alfano, Megan A Iammarino, Natalie F Reash, et al.
Nature Medicine
|
January 4, 2024
Gene therapy with bidridistrogene xeboparvovec for limb-girdle muscular dystrophy type 2E/R4: phase 1/2 trial results
Jerry R Mendell, Eric R Pozsgai, Sarah Lewis, et al.
Muscle & Nerve
|
August 14, 2023
Long-term safety and functional outcomes of delandistrogene moxeparvovec gene therapy in patients with Duchenne muscular dystrophy: A phase 1/2a nonrandomized trial
Jerry R Mendell, Zarife Sahenk, Kelly J Lehman, et al.
Journal of Neuromuscular Diseases
|
February 20, 2025
Gross motor delays in infants and young boys with Duchenne muscular dystrophy
Linda P Lowes, Natalie F Reash, Megan A Iammarino, et al.
Muscle & Nerve
|
May 4, 2022
Comparison of strength testing modalities in dysferlinopathy
Natalie F Reash, Meredith K James, Lindsay N Alfano, et al.
Neurology. Genetics
|
November 3, 2025
Motor Function in Limb-Girdle Muscular Dystrophy R1/2A: Validation of Clinical Outcome Assessments for Clinical Care and Trial Readiness
Meredith K James, Megan A Iammarino, Natalie F Reash, et al.
Frontiers in Cell and Developmental Biology
|
July 27, 2023
Expression of SRP-9001 dystrophin and stabilization of motor function up to 2 years post-treatment with delandistrogene moxeparvovec gene therapy in individuals with Duchenne muscular dystrophy
Jerry R Mendell, Perry B Shieh, Craig M McDonald, et al.
Annals of Clinical and Translational Neurology
|
April 16, 2025
Clinical Trial Readiness in Limb Girdle Muscular Dystrophy R1 (LGMDR1): A GRASP Consortium Study
Stephanie M Hunn, Lindsay N Alfano, Aileen Jones, et al.
Annals of Clinical and Translational Neurology
|
December 15, 2024
Prospective observational study of FKRP-related limb-girdle muscular dystrophy R9: A GRASP consortium study
Lindsay N Alfano, Meredith K James, Kristine Grosfjeld Petersen, et al.
Neuromuscular Disorders : NMD
|
April 10, 2026
Natural history of limb girdle muscular dystrophy R1 (LGMDR1): a GRASP consortium study
Stephanie M Hunn, Andrew R Findlay, Lindsay N Alfano, et al.
Page
of 2