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Nina Butoianu

Showing results (1-10 of 5) with videos related to

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Neuromuscular Disorders : NMD|August 14, 2017
DMD and West syndromeRuxandra Cardas, Catrinel Iliescu, Nina Butoianu, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society|August 9, 2020
European ad-hoc consensus statement on gene replacement therapy for spinal muscular atrophyJanbernd Kirschner, Nina Butoianu, Nathalie Goemans, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society|June 15, 2024
2024 update: European consensus statement on gene therapy for spinal muscular atrophyJanbernd Kirschner, Günther Bernert, Nina Butoianu, et al.
Journal of Neuromuscular Diseases|November 19, 2016
Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe PhenotypeLaurent Servais, Marie Montus, Caroline Le Guiner, et al.
Scientific Reports|November 29, 2024
Evidentiary basis of the first regulatory qualification of a digital primary efficacy endpointLaurent Servais, Paul Strijbos, Margaux Poleur, et al.
Pageof 1

Showing results (1-10 of 5) with videos related to

Sort By:
Pageof 1
Neuromuscular Disorders : NMD|August 14, 2017
DMD and West syndromeRuxandra Cardas, Catrinel Iliescu, Nina Butoianu, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society|August 9, 2020
European ad-hoc consensus statement on gene replacement therapy for spinal muscular atrophyJanbernd Kirschner, Nina Butoianu, Nathalie Goemans, et al.
European Journal of Paediatric Neurology : EJPN : Official Journal of the European Paediatric Neurology Society|June 15, 2024
2024 update: European consensus statement on gene therapy for spinal muscular atrophyJanbernd Kirschner, Günther Bernert, Nina Butoianu, et al.
Journal of Neuromuscular Diseases|November 19, 2016
Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe PhenotypeLaurent Servais, Marie Montus, Caroline Le Guiner, et al.
Scientific Reports|November 29, 2024
Evidentiary basis of the first regulatory qualification of a digital primary efficacy endpointLaurent Servais, Paul Strijbos, Margaux Poleur, et al.
Pageof 1