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DNA and Cell Biology
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November 22, 2002
Helios gene gun particle delivery for therapy of acid maltase deficiency
Frank Martiniuk, Agnes Chen, Adra Mack, et al.
Orphanet Journal of Rare Diseases
|
June 22, 2013
Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy
Sean N Prater, Trusha T Patel, Anne F Buckley, et al.
Arthritis and Rheumatism
|
July 20, 2011
The role of TRAIL in mediating autophagy in myositis skeletal muscle: a potential nonimmune mechanism of muscle damage
Heather M Alger, Nina Raben, Emidio Pistilli, et al.
Acta Neuropathologica Communications
|
January 4, 2014
The value of muscle biopsies in Pompe disease: identifying lipofuscin inclusions in juvenile- and adult-onset patients
Erin J Feeney, Stephanie Austin, Yin-Hsiu Chien, et al.
EMBO Molecular Medicine
|
April 23, 2013
Transcription factor EB (TFEB) is a new therapeutic target for Pompe disease
Carmine Spampanato, Erin Feeney, Lishu Li, et al.
Journal of Neuropathology and Experimental Neurology
|
July 24, 2008
Temporal neuropathologic and behavioral phenotype of 6neo/6neo Pompe disease mice
Richard L Sidman, Tatyana Taksir, Jonathan Fidler, et al.
Autophagy
|
May 13, 2016
TFEB and TFE3 cooperate in the regulation of the innate immune response in activated macrophages
Nunzia Pastore, Owen A Brady, Heba I Diab, et al.
Human Molecular Genetics
|
December 5, 2009
Restoration of muscle functionality by genetic suppression of glycogen synthesis in a murine model of Pompe disease
Gaelle Douillard-Guilloux, Nina Raben, Shoichi Takikita, et al.
Autophagy
|
September 24, 2010
Suppression of autophagy permits successful enzyme replacement therapy in a lysosomal storage disorder--murine Pompe disease
Nina Raben, Cynthia Schreiner, Rebecca Baum, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 9, 2004
Replacing acid alpha-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers
Nina Raben, Tokiko Fukuda, Abigail L Gilbert, et al.
Page
of 8
Search research articles
Search
Showing results (51-60 of 72) with videos related to
Sort By:
Page
of 8
DNA and Cell Biology
|
November 22, 2002
Helios gene gun particle delivery for therapy of acid maltase deficiency
Frank Martiniuk, Agnes Chen, Adra Mack, et al.
Orphanet Journal of Rare Diseases
|
June 22, 2013
Skeletal muscle pathology of infantile Pompe disease during long-term enzyme replacement therapy
Sean N Prater, Trusha T Patel, Anne F Buckley, et al.
Arthritis and Rheumatism
|
July 20, 2011
The role of TRAIL in mediating autophagy in myositis skeletal muscle: a potential nonimmune mechanism of muscle damage
Heather M Alger, Nina Raben, Emidio Pistilli, et al.
Acta Neuropathologica Communications
|
January 4, 2014
The value of muscle biopsies in Pompe disease: identifying lipofuscin inclusions in juvenile- and adult-onset patients
Erin J Feeney, Stephanie Austin, Yin-Hsiu Chien, et al.
EMBO Molecular Medicine
|
April 23, 2013
Transcription factor EB (TFEB) is a new therapeutic target for Pompe disease
Carmine Spampanato, Erin Feeney, Lishu Li, et al.
Journal of Neuropathology and Experimental Neurology
|
July 24, 2008
Temporal neuropathologic and behavioral phenotype of 6neo/6neo Pompe disease mice
Richard L Sidman, Tatyana Taksir, Jonathan Fidler, et al.
Autophagy
|
May 13, 2016
TFEB and TFE3 cooperate in the regulation of the innate immune response in activated macrophages
Nunzia Pastore, Owen A Brady, Heba I Diab, et al.
Human Molecular Genetics
|
December 5, 2009
Restoration of muscle functionality by genetic suppression of glycogen synthesis in a murine model of Pompe disease
Gaelle Douillard-Guilloux, Nina Raben, Shoichi Takikita, et al.
Autophagy
|
September 24, 2010
Suppression of autophagy permits successful enzyme replacement therapy in a lysosomal storage disorder--murine Pompe disease
Nina Raben, Cynthia Schreiner, Rebecca Baum, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 9, 2004
Replacing acid alpha-glucosidase in Pompe disease: recombinant and transgenic enzymes are equipotent, but neither completely clears glycogen from type II muscle fibers
Nina Raben, Tokiko Fukuda, Abigail L Gilbert, et al.
Page
of 8