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Frontiers in Pediatrics
|
April 24, 2025
Evaluating treatment and care outcomes for neuromuscular diseases in a pediatric intermediate care setting
Giacomo Brisca, Marina F Strati, Francesca Canzoneri, et al.
Frontiers in Pediatrics
|
July 28, 2022
Acute Neurological Presentation in Children With SARS-CoV-2 Infection
Antonella Riva, Gianluca Piccolo, Federica Balletti, et al.
Molecular Neurobiology
|
May 5, 2025
Exploratory Analysis of Gut Microbiota Profile in Duchenne Muscular Dystrophy (DMD) Patients with Intellectual Disability
Chiara Panicucci, Sara Casalini, Giovanni Fiorito, et al.
Biomedicines
|
January 20, 2021
Musculoskeletal Features without Ataxia Associated with a Novel de novo Mutation in <i>KCNA1</i> Impairing the Voltage Sensitivity of Kv1.1 Channel
Paola Imbrici, Andrea Accogli, Rikard Blunck, et al.
Nutrition (Burbank, Los Angeles County, Calif.)
|
July 6, 2019
Non-interventional, retrospective data of long-term home parenteral nutrition in patients with benign diseases: Analysis of a nurse register (SERECARE)
Antonella De Francesco, Antonella Diamanti, Paolo Gandullia, et al.
Cellular and Molecular Life Sciences : CMLS
|
September 10, 2024
Proteomics profiling and machine learning in nusinersen-treated patients with spinal muscular atrophy
Chiara Panicucci, Eray Sahin, Martina Bartolucci, et al.
Molecular Genetics & Genomic Medicine
|
August 7, 2025
Functional Characterization of a Novel Intronic Variant in PIEZO2 in a Recessive Form of Distal Arthrogryposis With Impaired Proprioception and Touch (DAIPT)
Michela Bellardita, Ferruccio Romano, Ludovica Menta, et al.
Neuromuscular Disorders : NMD
|
December 1, 2022
Long term follow-up of scoliosis progression in type II SMA patients
Giorgia Coratti, Maria Carmela Pera, Adele D'Amico, et al.
Archives of Disease in Childhood
|
January 30, 2024
Communicative development inventory in type 1 and presymptomatic infants with spinal muscular atrophy: a cohort study
Bianca Buchignani, Gianpaolo Cicala, Francesca Cumbo, et al.
Neurological Sciences : Official Journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology
|
March 28, 2025
Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data
Emilio Albamonte, Adrea Lizio, Giorgia Coratti, et al.
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Search research articles
Search
Showing results (11-20 of 35) with videos related to
Sort By:
Page
of 4
Frontiers in Pediatrics
|
April 24, 2025
Evaluating treatment and care outcomes for neuromuscular diseases in a pediatric intermediate care setting
Giacomo Brisca, Marina F Strati, Francesca Canzoneri, et al.
Frontiers in Pediatrics
|
July 28, 2022
Acute Neurological Presentation in Children With SARS-CoV-2 Infection
Antonella Riva, Gianluca Piccolo, Federica Balletti, et al.
Molecular Neurobiology
|
May 5, 2025
Exploratory Analysis of Gut Microbiota Profile in Duchenne Muscular Dystrophy (DMD) Patients with Intellectual Disability
Chiara Panicucci, Sara Casalini, Giovanni Fiorito, et al.
Biomedicines
|
January 20, 2021
Musculoskeletal Features without Ataxia Associated with a Novel de novo Mutation in <i>KCNA1</i> Impairing the Voltage Sensitivity of Kv1.1 Channel
Paola Imbrici, Andrea Accogli, Rikard Blunck, et al.
Nutrition (Burbank, Los Angeles County, Calif.)
|
July 6, 2019
Non-interventional, retrospective data of long-term home parenteral nutrition in patients with benign diseases: Analysis of a nurse register (SERECARE)
Antonella De Francesco, Antonella Diamanti, Paolo Gandullia, et al.
Cellular and Molecular Life Sciences : CMLS
|
September 10, 2024
Proteomics profiling and machine learning in nusinersen-treated patients with spinal muscular atrophy
Chiara Panicucci, Eray Sahin, Martina Bartolucci, et al.
Molecular Genetics & Genomic Medicine
|
August 7, 2025
Functional Characterization of a Novel Intronic Variant in PIEZO2 in a Recessive Form of Distal Arthrogryposis With Impaired Proprioception and Touch (DAIPT)
Michela Bellardita, Ferruccio Romano, Ludovica Menta, et al.
Neuromuscular Disorders : NMD
|
December 1, 2022
Long term follow-up of scoliosis progression in type II SMA patients
Giorgia Coratti, Maria Carmela Pera, Adele D'Amico, et al.
Archives of Disease in Childhood
|
January 30, 2024
Communicative development inventory in type 1 and presymptomatic infants with spinal muscular atrophy: a cohort study
Bianca Buchignani, Gianpaolo Cicala, Francesca Cumbo, et al.
Neurological Sciences : Official Journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology
|
March 28, 2025
Patients on treatment with risdiplam in Italy: challenges in the interpretation of the real-world data
Emilio Albamonte, Adrea Lizio, Giorgia Coratti, et al.
Page
of 4