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JAMA Neurology|March 16, 2026
Safety and Efficacy of PrimeC in Amyotrophic Lateral Sclerosis: The PARADIGM Randomized Clinical TrialMerit Cudkowicz, Vivian E Drory, Adriano Chio, et al.
Neurology. Genetics|September 15, 2022
Phenotype Analysis of Fused in Sarcoma Mutations in Amyotrophic Lateral SclerosisMaurizio Grassano, Giorgia Brodini, Giovanni De Marco, et al.
Amyotrophic Lateral Sclerosis : Official Publication of the World Federation of Neurology Research Group on Motor Neuron Diseases|February 27, 2010
Guidelines for preclinical animal research in ALS/MND: A consensus meetingAlbert C Ludolph, Caterina Bendotti, Eran Blaugrund, et al.
Human Molecular Genetics|February 4, 2017
C9ORF72 hexanucleotide repeat exerts toxicity in a stable, inducible motor neuronal cell model, which is rescued by partial depletion of PtenMatthew J Stopford, Adrian Higginbottom, Guillaume M Hautbergue, et al.
The Journal of Neuroscience : the Official Journal of the Society for Neuroscience|December 8, 2021
GCH1 Deficiency Activates Brain Innate Immune Response and Impairs Tyrosine Hydroxylase HomeostasisHannah Larbalestier, Marcus Keatinge, Lisa Watson, et al.
Movement Disorders : Official Journal of the Movement Disorder Society|July 13, 2019
The genetic and clinico-pathological profile of early-onset progressive supranuclear palsyEdwin Jabbari, John Woodside, Manuela M X Tan, et al.
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