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Gastroenterology|December 6, 2014
Truncating mutation in the nitric oxide synthase 1 gene is associated with infantile achalasiaEyal Shteyer, Simon Edvardson, Sarah L Wynia-Smith, et al.
The Journal of Experimental Medicine|June 1, 2016
Early onset combined immunodeficiency and autoimmunity in patients with loss-of-function mutation in LATBaerbel Keller, Irina Zaidman, O Sascha Yousefi, et al.
Molecular Genetics and Metabolism|May 28, 2013
Exome sequencing identifies a new mutation in SERAC1 in a patient with 3-methylglutaconic aciduriaFrederic Tort, María Teresa García-Silva, Xènia Ferrer-Cortès, et al.
American Journal of Human Genetics|March 21, 2017
Mutations in TMEM260 Cause a Pediatric Neurodevelopmental, Cardiac, and Renal SyndromeAsaf Ta-Shma, Tahir N Khan, Asaf Vivante, et al.
Journal of Clinical Immunology|December 19, 2023
Combined Immunodeficiency Caused by a Novel Nonsense Mutation in LCKBaerbel Keller, Shlomit Kfir-Erenfeld, Paul Matusewicz, et al.
The Journal of Allergy and Clinical Immunology|February 5, 2013
Deficiency of caspase recruitment domain family, member 11 (CARD11), causes profound combined immunodeficiency in human subjectsPolina Stepensky, Baerbel Keller, Mary Buchta, et al.
American Journal of Human Genetics|October 19, 2010
Infantile cerebral and cerebellar atrophy is associated with a mutation in the MED17 subunit of the transcription preinitiation mediator complexRami Kaufmann, Rachel Straussberg, Hanna Mandel, et al.
Journal of Medical Genetics|December 29, 2022
Consolidating the association of biallelic <i>MAPKAPK5</i> pathogenic variants with a distinct syndromic neurodevelopmental disorderReza Maroofian, Stephanie Efthymiou, Mohnish Suri, et al.
Journal of Medical Genetics|October 4, 2016
Mutations in the phosphatidylinositol glycan C (<i>PIGC</i>) gene are associated with epilepsy and intellectual disabilitySimon Edvardson, Yoshiko Murakami, Thi Tuyet Mai Nguyen, et al.
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