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European Journal of Neurology|September 23, 2022
Effect of RNS60 in amyotrophic lateral sclerosis: a phase II multicentre, randomized, double-blind, placebo-controlled trialEttore Beghi, Elisabetta Pupillo, Elisa Bianchi, et al.Journal of Neurology, Neurosurgery, and Psychiatry|May 16, 2022
Effect of sodium phenylbutyrate/taurursodiol on tracheostomy/ventilation-free survival and hospitalisation in amyotrophic lateral sclerosis: long-term results from the CENTAUR trialSabrina Paganoni, Suzanne Hendrix, Samuel P Dickson, et al.The New England Journal of Medicine|September 3, 2020
Trial of Sodium Phenylbutyrate-Taurursodiol for Amyotrophic Lateral SclerosisSabrina Paganoni, Eric A Macklin, Suzanne Hendrix, et al.Muscle & Nerve|October 16, 2020
Long-term survival of participants in the CENTAUR trial of sodium phenylbutyrate-taurursodiol in amyotrophic lateral sclerosisSabrina Paganoni, Suzanne Hendrix, Samuel P Dickson, et al.JAMA Network Open|February 17, 2025
Efficacy and Safety of Zilucoplan in Amyotrophic Lateral Sclerosis: A Randomized Clinical TrialSabrina Paganoni, Christina N Fournier, Eric A Macklin, et al.JAMA|March 11, 2025
Pridopidine in Amyotrophic Lateral Sclerosis: The HEALEY ALS Platform Trial, Jeremy M Shefner, Björn Oskarsson, et al.Nature Neuroscience|February 4, 2022
Answer ALS, a large-scale resource for sporadic and familial ALS combining clinical and multi-omics data from induced pluripotent cell linesEmily G Baxi, Terri Thompson, Jonathan Li, et al.Pageof 9