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Neurology
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May 26, 2022
Long-term Safety and Efficacy of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease
Mazen M Dimachkie, Richard J Barohn, Barry Byrne, et al.
European Journal of Neurology
|
October 27, 2025
Causes of Death and Comorbidities in Adult Patients With Late-Onset Pompe Disease: A French Pompe Registry Retrospective Study
Diana Maria Chitimus, Céline Tard, Maxime Fournier, et al.
Neuroimage. Clinical
|
December 8, 2018
The spinal and cerebral profile of adult spinal-muscular atrophy: A multimodal imaging study
Giorgia Querin, Mohamed-Mounir El Mendili, Timothée Lenglet, et al.
Annals of Neurology
|
October 5, 2012
Adult polyglucosan body disease: Natural History and Key Magnetic Resonance Imaging Findings
Fanny Mochel, Raphael Schiffmann, Marjan E Steenweg, et al.
Neurology
|
July 7, 2023
Characteristics of Patients With Late-Onset Pompe Disease in France: Insights From the French Pompe Registry in 2022
Claire Lefeuvre, Marie De Antonio, Francoise Bouhour, et al.
European Journal of Neurology
|
August 7, 2024
Bulbar muscle impairment in patients with late onset Pompe disease: Insight from the French Pompe registry
Emilie Retailleau, Claire Lefeuvre, Marie De Antonio, et al.
Orphanet Journal of Rare Diseases
|
November 25, 2020
Data from the European registry for patients with McArdle disease and other muscle glycogenoses (EUROMAC)
Renata S Scalco, Alejandro Lucia, Alfredo Santalla, et al.
Brain : a Journal of Neurology
|
January 14, 2012
A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
Serge Herson, Faycal Hentati, Aude Rigolet, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
April 23, 2013
Hereditary myopathy with early respiratory failure: occurrence in various populations
Johanna Palmio, Anni Evilä, Françoise Chapon, et al.
Orphanet Journal of Rare Diseases
|
July 24, 2023
Data from the European registry for patients with McArdle disease (EUROMAC): functional status and social participation
Walaa Karazi, Renata S Scalco, Mads G Stemmerik, et al.
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of 17
Search research articles
Search
Showing results (141-150 of 164) with videos related to
Sort By:
Page
of 17
Neurology
|
May 26, 2022
Long-term Safety and Efficacy of Avalglucosidase Alfa in Patients With Late-Onset Pompe Disease
Mazen M Dimachkie, Richard J Barohn, Barry Byrne, et al.
European Journal of Neurology
|
October 27, 2025
Causes of Death and Comorbidities in Adult Patients With Late-Onset Pompe Disease: A French Pompe Registry Retrospective Study
Diana Maria Chitimus, Céline Tard, Maxime Fournier, et al.
Neuroimage. Clinical
|
December 8, 2018
The spinal and cerebral profile of adult spinal-muscular atrophy: A multimodal imaging study
Giorgia Querin, Mohamed-Mounir El Mendili, Timothée Lenglet, et al.
Annals of Neurology
|
October 5, 2012
Adult polyglucosan body disease: Natural History and Key Magnetic Resonance Imaging Findings
Fanny Mochel, Raphael Schiffmann, Marjan E Steenweg, et al.
Neurology
|
July 7, 2023
Characteristics of Patients With Late-Onset Pompe Disease in France: Insights From the French Pompe Registry in 2022
Claire Lefeuvre, Marie De Antonio, Francoise Bouhour, et al.
European Journal of Neurology
|
August 7, 2024
Bulbar muscle impairment in patients with late onset Pompe disease: Insight from the French Pompe registry
Emilie Retailleau, Claire Lefeuvre, Marie De Antonio, et al.
Orphanet Journal of Rare Diseases
|
November 25, 2020
Data from the European registry for patients with McArdle disease and other muscle glycogenoses (EUROMAC)
Renata S Scalco, Alejandro Lucia, Alfredo Santalla, et al.
Brain : a Journal of Neurology
|
January 14, 2012
A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
Serge Herson, Faycal Hentati, Aude Rigolet, et al.
Journal of Neurology, Neurosurgery, and Psychiatry
|
April 23, 2013
Hereditary myopathy with early respiratory failure: occurrence in various populations
Johanna Palmio, Anni Evilä, Françoise Chapon, et al.
Orphanet Journal of Rare Diseases
|
July 24, 2023
Data from the European registry for patients with McArdle disease (EUROMAC): functional status and social participation
Walaa Karazi, Renata S Scalco, Mads G Stemmerik, et al.
Page
of 17