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Eclinicalmedicine
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June 13, 2025
Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial
Ángeles García-Cazorla, Caroline Sevin, Juliana Ribeiro Constante, et al.
Nature Communications
|
September 4, 2024
Cannabidiol ameliorates mitochondrial disease via PPARγ activation in preclinical models
Emma Puighermanal, Marta Luna-Sánchez, Alejandro Gella, et al.
Bioorganic & Medicinal Chemistry Letters
|
August 21, 2018
Squaramides as novel class I and IIB histone deacetylase inhibitors for topical treatment of cutaneous t-cell lymphoma
Jean-François Fournier, Yushma Bhurruth-Alcor, Branislav Musicki, et al.
Journal of Medicinal Chemistry
|
April 13, 2018
Rational Drug Design of Topically Administered Caspase 1 Inhibitors for the Treatment of Inflammatory Acne
Jean-François Fournier, Laurence Clary, Sandrine Chambon, et al.
3D Printing in Medicine
|
April 23, 2021
Point-of-care manufacturing: a single university hospital's initial experience
Jose Antonio Calvo-Haro, Javier Pascau, José Manuel Asencio-Pascual, et al.
Bioorganic & Medicinal Chemistry
|
August 19, 2017
Discovery and process development of a novel TACE inhibitor for the topical treatment of psoriasis
Jean-Guy Boiteau, Gilles Ouvry, Jean-Marie Arlabosse, et al.
Orphanet Journal of Rare Diseases
|
March 11, 2025
Pregnancy-related issues in rare and low-prevalence diseases: results of ERN transversal working group on pregnancy and family planning survey
Dina Zucchi, Diana Marinello, Chiara Tani, et al.
Reproductive Health
|
November 26, 2025
Addressing unmet needs in pregnancy and family planning of people living with rare and low-prevalence diseases: results of the "ERN transversal working group on pregnancy and family planning" survey
Giovanni Fulvio, Diana Marinello, Dina Zucchi, et al.
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of 15
Search research articles
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Showing results (141-150 of 148) with videos related to
Sort By:
Page
of 15
You have reached the last page of results.
This site can display upto 148 results.
Eclinicalmedicine
|
June 13, 2025
Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial
Ángeles García-Cazorla, Caroline Sevin, Juliana Ribeiro Constante, et al.
Nature Communications
|
September 4, 2024
Cannabidiol ameliorates mitochondrial disease via PPARγ activation in preclinical models
Emma Puighermanal, Marta Luna-Sánchez, Alejandro Gella, et al.
Bioorganic & Medicinal Chemistry Letters
|
August 21, 2018
Squaramides as novel class I and IIB histone deacetylase inhibitors for topical treatment of cutaneous t-cell lymphoma
Jean-François Fournier, Yushma Bhurruth-Alcor, Branislav Musicki, et al.
Journal of Medicinal Chemistry
|
April 13, 2018
Rational Drug Design of Topically Administered Caspase 1 Inhibitors for the Treatment of Inflammatory Acne
Jean-François Fournier, Laurence Clary, Sandrine Chambon, et al.
3D Printing in Medicine
|
April 23, 2021
Point-of-care manufacturing: a single university hospital's initial experience
Jose Antonio Calvo-Haro, Javier Pascau, José Manuel Asencio-Pascual, et al.
Bioorganic & Medicinal Chemistry
|
August 19, 2017
Discovery and process development of a novel TACE inhibitor for the topical treatment of psoriasis
Jean-Guy Boiteau, Gilles Ouvry, Jean-Marie Arlabosse, et al.
Orphanet Journal of Rare Diseases
|
March 11, 2025
Pregnancy-related issues in rare and low-prevalence diseases: results of ERN transversal working group on pregnancy and family planning survey
Dina Zucchi, Diana Marinello, Chiara Tani, et al.
Reproductive Health
|
November 26, 2025
Addressing unmet needs in pregnancy and family planning of people living with rare and low-prevalence diseases: results of the "ERN transversal working group on pregnancy and family planning" survey
Giovanni Fulvio, Diana Marinello, Dina Zucchi, et al.
Page
of 15