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Drug Delivery and Translational Research
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March 20, 2015
Delivering drugs to the central nervous system: an overview
Patricia I Dickson
Molecular Genetics and Metabolism
|
December 3, 2014
The individual (single patient) IND for inborn errors of metabolism
Patricia I Dickson, Jakub Tolar
Current Pharmaceutical Biotechnology
|
April 22, 2011
Intrathecal enzyme replacement therapy for mucopolysaccharidosis I: translating success in animal models to patients
Patricia I Dickson, Agnes H Chen
Journal of Inherited Metabolic Disease
|
June 30, 2021
Mucopolysaccharidoses type I gene therapy
Sarah C Hurt, Patricia I Dickson, David T Curiel
American Journal of Medical Genetics. Part A
|
February 20, 2025
Single-Gene Deletion of FGF3 in a Patient With Features of 11q13 Microdeletion Syndrome
Hamed Rahi, Patricia I Dickson, Tomi L Toler, et al.
European Journal of Medical Genetics
|
April 29, 2022
Diagnostic yield of exome sequencing in congenital vertical talus
Naeimeh Tayebi, Wu-Lin Charng, Patricia I Dickson, et al.
Nature Reviews. Neurology
|
September 4, 2025
Neuronal ceroid lipofuscinosis: underlying mechanisms and emerging therapeutic targets
Ewa A Ziółkowska, Keigo Takahashi, Patricia I Dickson, et al.
Disease Markers
|
February 12, 2013
WITHDRAWN: Glycan-based biomarkers for mucopolysaccharidoses
Roger Lawrence, Jillian R Brown, Fred Lorey, et al.
Molecular Genetics and Metabolism
|
August 21, 2013
Glycan-based biomarkers for mucopolysaccharidoses
Roger Lawrence, Jillian R Brown, Fred Lorey, et al.
JIMD Reports
|
November 18, 2020
Fatal COVID-19 infection in a patient with long-chain 3-hydroxyacyl-CoA dehydrogenase deficiency: A case report
Parith Wongkittichote, James R Watson, Jennifer M Leonard, et al.
Page
of 8
Search research articles
Search
Showing results (1-10 of 72) with videos related to
Sort By:
Page
of 8
Drug Delivery and Translational Research
|
March 20, 2015
Delivering drugs to the central nervous system: an overview
Patricia I Dickson
Molecular Genetics and Metabolism
|
December 3, 2014
The individual (single patient) IND for inborn errors of metabolism
Patricia I Dickson, Jakub Tolar
Current Pharmaceutical Biotechnology
|
April 22, 2011
Intrathecal enzyme replacement therapy for mucopolysaccharidosis I: translating success in animal models to patients
Patricia I Dickson, Agnes H Chen
Journal of Inherited Metabolic Disease
|
June 30, 2021
Mucopolysaccharidoses type I gene therapy
Sarah C Hurt, Patricia I Dickson, David T Curiel
American Journal of Medical Genetics. Part A
|
February 20, 2025
Single-Gene Deletion of FGF3 in a Patient With Features of 11q13 Microdeletion Syndrome
Hamed Rahi, Patricia I Dickson, Tomi L Toler, et al.
European Journal of Medical Genetics
|
April 29, 2022
Diagnostic yield of exome sequencing in congenital vertical talus
Naeimeh Tayebi, Wu-Lin Charng, Patricia I Dickson, et al.
Nature Reviews. Neurology
|
September 4, 2025
Neuronal ceroid lipofuscinosis: underlying mechanisms and emerging therapeutic targets
Ewa A Ziółkowska, Keigo Takahashi, Patricia I Dickson, et al.
Disease Markers
|
February 12, 2013
WITHDRAWN: Glycan-based biomarkers for mucopolysaccharidoses
Roger Lawrence, Jillian R Brown, Fred Lorey, et al.
Molecular Genetics and Metabolism
|
August 21, 2013
Glycan-based biomarkers for mucopolysaccharidoses
Roger Lawrence, Jillian R Brown, Fred Lorey, et al.
JIMD Reports
|
November 18, 2020
Fatal COVID-19 infection in a patient with long-chain 3-hydroxyacyl-CoA dehydrogenase deficiency: A case report
Parith Wongkittichote, James R Watson, Jennifer M Leonard, et al.
Page
of 8