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Current Gene Therapy|April 9, 2008
Viral vectors in cancer immunotherapy: which vector for which strategy?Sara A Collins, Barbara-Ann Guinn, Patrick T Harrison, et al.Immunology|October 18, 2002
C-reactive protein-mediated phagocytosis and phospholipase D signalling through the high-affinity receptor for immunoglobulin G (FcgammaRI)Katherine B Bodman-Smith, Alirio J Melendez, Ian Campbell, et al.Genetic Vaccines and Therapy|December 22, 2010
AAV2-mediated in vivo immune gene therapy of solid tumoursSara A Collins, Alexandra Buhles, Martina F Scallan, et al.Cell & Bioscience|February 10, 2023
Mutation-class dependent signatures outweigh disease-associated processes in cystic fibrosis cellsLúcia Santos, Rui Nascimento, Aires Duarte, et al.Journal of Cystic Fibrosis : Official Journal of the European Cystic Fibrosis Society|June 9, 2021
Comparison of Cas9 and Cas12a CRISPR editing methods to correct the W1282X-CFTR mutationLúcia Santos, Karen Mention, Kader Cavusoglu-Doran, et al.Journal of the American Society of Nephrology : JASN|March 22, 2020
Use of Human Induced Pluripotent Stem Cells and Kidney Organoids To Develop a Cysteamine/mTOR Inhibition Combination Therapy for CystinosisJennifer A Hollywood, Aneta Przepiorski, Randall F D'Souza, et al.Journal of Molecular Neuroscience : MN|March 16, 2018
The Regulation of Monoamine Oxidase A Gene Expression by Distinct Variable Number Tandem RepeatsMaurizio Manca, Veridiana Pessoa, Ana Illera Lopez, et al.Pediatric Pulmonology|September 24, 2016
Genetic medicines for CF: Hype versus realityEric W F W Alton, A Christopher Boyd, Jane C Davies, et al.Molecular Therapy. Methods & Clinical Development|November 29, 2023
Molecular and functional correction of a deep intronic splicing mutation in CFTR by CRISPR-Cas9 gene editingAmy J Walker, Carina Graham, Miriam Greenwood, et al.Human Molecular Genetics|August 31, 2023
Use of adenine base editing and homology-independent targeted integration strategies to correct the cystic fibrosis causing variant, W1282XKaren Mention, Kader Cavusoglu-Doran, Anya T Joynt, et al.Pageof 6