Showing results (1-10 of 89) with videos related to
Sort By:
Pageof 9
Bioessays : News and Reviews in Molecular, Cellular and Developmental Biology|March 6, 2025
AAV Genome Topology Decides ITR Secondary StructurePatrick Wilmott, Leszek LisowskiHuman Gene Therapy Methods|November 23, 2019
A User's Guide to the Inverted Terminal Repeats of Adeno-Associated VirusPatrick Wilmott, Leszek Lisowski, Ian E Alexander, et al.Methods in Molecular Biology (Clifton, N.J.)|April 22, 2026
Selecting Novel Retino-tropic AAV Capsids by Directed EvolutionAdrian Westhaus, Leszek LisowskiBritish Journal of Haematology|April 16, 2008
Current status of globin gene therapy for the treatment of beta-thalassaemiaLeszek Lisowski, Michel SadelainBlood|October 9, 2007
Locus control region elements HS1 and HS4 enhance the therapeutic efficacy of globin gene transfer in beta-thalassemic miceLeszek Lisowski, Michel SadelainMolecular Therapy : the Journal of the American Society of Gene Therapy|October 22, 2009
Supplying clotting factors from hematopoietic stem cell-derived erythroid and megakaryocytic lineage cellsMichel Sadelain, Alex Chang, Leszek LisowskiCurrent Opinion in Pharmacology|August 21, 2015
Adeno-associated virus serotypes for gene therapeuticsLeszek Lisowski, Szun Szun Tay, Ian Edward AlexanderMedicinal Research Reviews|February 14, 2023
Molecular mechanisms of amyotrophic lateral sclerosis as broad therapeutic targets for gene therapy applications utilizing adeno-associated viral vectorsJessica Merjane, Roger Chung, Rickie Patani, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|August 7, 2008
Erythroid-specific human factor IX delivery from in vivo selected hematopoietic stem cells following nonmyeloablative conditioning in hemophilia B miceAlex H Chang, Matthias T Stephan, Leszek Lisowski, et al.Best Practice & Research. Clinical Haematology|October 23, 2004
Globin gene transfer for treatment of the beta-thalassemias and sickle cell diseaseMichel Sadelain, Stefano Rivella, Leszek Lisowski, et al.Pageof 9