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Human Gene Therapy
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January 10, 2020
Can Adeno-Associated Viral Vectors Deliver Effectively Large Genes?
Patrizia Tornabene, Ivana Trapani
European Journal of Cell Biology
|
November 1, 2024
Exploring optimal protocols for generating and preserving glucose-responsive insulin-secreting progenitor cells derived from human pluripotent stem cells
Patrizia Tornabene, James M Wells
Gene Therapy
|
July 15, 2020
Large gene delivery to the retina with AAV vectors: are we there yet?
Ivana Trapani, Patrizia Tornabene, Alberto Auricchio
Advanced Drug Delivery Reviews
|
March 7, 2026
Microphysiological systems to accelerate and De-risk AAV Gene therapy development
Patrizia Tornabene, Estelle Berreur, Adrian Roth, et al.
Biorxiv : the Preprint Server for Biology
|
November 24, 2025
Human pancreatic organoids derived from pluripotent stem cells recapitulate pancreatic organogenesis
Jonathan A Brassard, Patrizia Tornabene, Daniel O Kechele, et al.
Molecular Therapy. Methods & Clinical Development
|
November 17, 2021
Inclusion of a degron reduces levelsof undesired inteins after AAV-mediated protein<i>trans-</i>splicing in the retina
Patrizia Tornabene, Ivana Trapani, Miriam Centrulo, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 3, 2018
Triple Vectors Expand AAV Transfer Capacity in the Retina
Andrea Maddalena, Patrizia Tornabene, Paola Tiberi, et al.
EMBO Molecular Medicine
|
May 2, 2022
Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A
Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, et al.
Human Gene Therapy
|
April 12, 2018
High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction In Vitro and in Mouse Retina
Andrea Maddalena, Fabio Dell'Aquila, Pia Giovannelli, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
April 15, 2026
Uncovering mitochondrial defects in photoreceptors opens therapeutic opportunities for Stargardt disease
Simona Brillante, Mariagrazia Volpe, Anna Diana, et al.
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of 2
Search research articles
Search
Showing results (1-10 of 12) with videos related to
Sort By:
Page
of 2
Human Gene Therapy
|
January 10, 2020
Can Adeno-Associated Viral Vectors Deliver Effectively Large Genes?
Patrizia Tornabene, Ivana Trapani
European Journal of Cell Biology
|
November 1, 2024
Exploring optimal protocols for generating and preserving glucose-responsive insulin-secreting progenitor cells derived from human pluripotent stem cells
Patrizia Tornabene, James M Wells
Gene Therapy
|
July 15, 2020
Large gene delivery to the retina with AAV vectors: are we there yet?
Ivana Trapani, Patrizia Tornabene, Alberto Auricchio
Advanced Drug Delivery Reviews
|
March 7, 2026
Microphysiological systems to accelerate and De-risk AAV Gene therapy development
Patrizia Tornabene, Estelle Berreur, Adrian Roth, et al.
Biorxiv : the Preprint Server for Biology
|
November 24, 2025
Human pancreatic organoids derived from pluripotent stem cells recapitulate pancreatic organogenesis
Jonathan A Brassard, Patrizia Tornabene, Daniel O Kechele, et al.
Molecular Therapy. Methods & Clinical Development
|
November 17, 2021
Inclusion of a degron reduces levelsof undesired inteins after AAV-mediated protein<i>trans-</i>splicing in the retina
Patrizia Tornabene, Ivana Trapani, Miriam Centrulo, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 3, 2018
Triple Vectors Expand AAV Transfer Capacity in the Retina
Andrea Maddalena, Patrizia Tornabene, Paola Tiberi, et al.
EMBO Molecular Medicine
|
May 2, 2022
Liver gene therapy with intein-mediated F8 trans-splicing corrects mouse haemophilia A
Federica Esposito, Hristiana Lyubenova, Patrizia Tornabene, et al.
Human Gene Therapy
|
April 12, 2018
High-Throughput Screening Identifies Kinase Inhibitors That Increase Dual Adeno-Associated Viral Vector Transduction In Vitro and in Mouse Retina
Andrea Maddalena, Fabio Dell'Aquila, Pia Giovannelli, et al.
Proceedings of the National Academy of Sciences of the United States of America
|
April 15, 2026
Uncovering mitochondrial defects in photoreceptors opens therapeutic opportunities for Stargardt disease
Simona Brillante, Mariagrazia Volpe, Anna Diana, et al.
Page
of 2