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The American Journal of Pathology
|
June 8, 2014
Abnormal splicing of NEDD4 in myotonic dystrophy type 2: possible link to statin adverse reactions
Mark Screen, Per Harald Jonson, Olayinka Raheem, et al.
Human Molecular Genetics
|
April 18, 2023
Extension of the DNAJB2a isoform in a dominant neuromyopathy family
Jaakko Sarparanta, Per Harald Jonson, Jens Reimann, et al.
Neuromuscular Disorders : NMD
|
September 5, 2015
Novel mutations in DNAJB6 gene cause a very severe early-onset limb-girdle muscular dystrophy 1D disease
Johanna Palmio, Per Harald Jonson, Anni Evilä, et al.
Journal of Neuromuscular Diseases
|
June 30, 2020
Identification and Characterization of Splicing Defects by Single-Molecule Real-Time Sequencing Technology (PacBio)
Marco Savarese, Talha Qureshi, Annalaura Torella, et al.
Annals of Neurology
|
February 13, 2013
Welander distal myopathy is caused by a mutation in the RNA-binding protein TIA1
Peter Hackman, Jaakko Sarparanta, Sara Lehtinen, et al.
Human Molecular Genetics
|
November 26, 2025
C-terminal extension of HSPB6 in a family with myopathy and cataract
Jaakko Sarparanta, Per Harald Jonson, Anna Vihola, et al.
Annals of Neurology
|
March 23, 2019
Actininopathy: A new muscular dystrophy caused by ACTN2 dominant mutations
Marco Savarese, Johanna Palmio, Juan José Poza, et al.
Neurology
|
March 8, 2019
An unusual ryanodine receptor 1 (RYR1) phenotype: Mild calf-predominant myopathy
Manu Jokela, Giorgio Tasca, Anna Vihola, et al.
Neurology. Genetics
|
November 1, 2021
Dominant Distal Myopathy 3 (MPD3) Caused by a Deletion in the <i>HNRNPA1</i> Gene
Peter Hackman, Salla M Rusanen, Mridul Johari, et al.
Neurology. Genetics
|
August 13, 2021
Out-of-Frame Mutations in <i>ACTN2</i> Last Exon Cause a Dominant Distal Myopathy With Facial Weakness
Marco Savarese, Anna Vihola, Manu E Jokela, et al.
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of 4
Search research articles
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Showing results (11-20 of 33) with videos related to
Sort By:
Page
of 4
The American Journal of Pathology
|
June 8, 2014
Abnormal splicing of NEDD4 in myotonic dystrophy type 2: possible link to statin adverse reactions
Mark Screen, Per Harald Jonson, Olayinka Raheem, et al.
Human Molecular Genetics
|
April 18, 2023
Extension of the DNAJB2a isoform in a dominant neuromyopathy family
Jaakko Sarparanta, Per Harald Jonson, Jens Reimann, et al.
Neuromuscular Disorders : NMD
|
September 5, 2015
Novel mutations in DNAJB6 gene cause a very severe early-onset limb-girdle muscular dystrophy 1D disease
Johanna Palmio, Per Harald Jonson, Anni Evilä, et al.
Journal of Neuromuscular Diseases
|
June 30, 2020
Identification and Characterization of Splicing Defects by Single-Molecule Real-Time Sequencing Technology (PacBio)
Marco Savarese, Talha Qureshi, Annalaura Torella, et al.
Annals of Neurology
|
February 13, 2013
Welander distal myopathy is caused by a mutation in the RNA-binding protein TIA1
Peter Hackman, Jaakko Sarparanta, Sara Lehtinen, et al.
Human Molecular Genetics
|
November 26, 2025
C-terminal extension of HSPB6 in a family with myopathy and cataract
Jaakko Sarparanta, Per Harald Jonson, Anna Vihola, et al.
Annals of Neurology
|
March 23, 2019
Actininopathy: A new muscular dystrophy caused by ACTN2 dominant mutations
Marco Savarese, Johanna Palmio, Juan José Poza, et al.
Neurology
|
March 8, 2019
An unusual ryanodine receptor 1 (RYR1) phenotype: Mild calf-predominant myopathy
Manu Jokela, Giorgio Tasca, Anna Vihola, et al.
Neurology. Genetics
|
November 1, 2021
Dominant Distal Myopathy 3 (MPD3) Caused by a Deletion in the <i>HNRNPA1</i> Gene
Peter Hackman, Salla M Rusanen, Mridul Johari, et al.
Neurology. Genetics
|
August 13, 2021
Out-of-Frame Mutations in <i>ACTN2</i> Last Exon Cause a Dominant Distal Myopathy With Facial Weakness
Marco Savarese, Anna Vihola, Manu E Jokela, et al.
Page
of 4