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Frontiers in Immunology
|
April 10, 2023
Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidase
Juliette Hordeaux, Ali Ramezani, Steve Tuske, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 10, 2006
Analysis of tumors arising in male B6C3F1 mice with and without AAV vector delivery to liver
Peter Bell, A David Moscioni, Robert J McCarter, et al.
Nature Biotechnology
|
November 6, 2023
Integrated vector genomes may contribute to long-term expression in primate liver after AAV administration
Jenny A Greig, Kelly M Martins, Camilo Breton, et al.
Molecular Genetics and Metabolism
|
July 9, 2016
Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model
Christian Hinderer, Peter Bell, Jean-Pierre Louboutin, et al.
Human Gene Therapy
|
August 16, 2017
Evaluation of Intrathecal Routes of Administration for Adeno-Associated Viral Vectors in Large Animals
Christian Hinderer, Peter Bell, Nathan Katz, et al.
Human Molecular Genetics
|
September 22, 2017
Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis
Christian Hinderer, Nathan Katz, Jean-Pierre Louboutin, et al.
Investigative Ophthalmology & Visual Science
|
July 19, 2012
RPGR-associated retinal degeneration in human X-linked RP and a murine model
Wei Chieh Huang, Alan F Wright, Alejandro J Roman, et al.
Science Advances
|
February 26, 2020
A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency
Lili Wang, Yang Yang, Camilo Breton, et al.
Nature Biotechnology
|
July 10, 2018
Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol
Lili Wang, Jeff Smith, Camilo Breton, et al.
Molecular Therapy. Methods & Clinical Development
|
February 25, 2022
Prednisolone reduces the interferon response to AAV in cynomolgus macaques and may increase liver gene expression
Lili Wang, Claude C Warzecha, Alexander Kistner, et al.
Page
of 11
Search research articles
Search
Showing results (91-100 of 105) with videos related to
Sort By:
Page
of 11
Frontiers in Immunology
|
April 10, 2023
Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidase
Juliette Hordeaux, Ali Ramezani, Steve Tuske, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 10, 2006
Analysis of tumors arising in male B6C3F1 mice with and without AAV vector delivery to liver
Peter Bell, A David Moscioni, Robert J McCarter, et al.
Nature Biotechnology
|
November 6, 2023
Integrated vector genomes may contribute to long-term expression in primate liver after AAV administration
Jenny A Greig, Kelly M Martins, Camilo Breton, et al.
Molecular Genetics and Metabolism
|
July 9, 2016
Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model
Christian Hinderer, Peter Bell, Jean-Pierre Louboutin, et al.
Human Gene Therapy
|
August 16, 2017
Evaluation of Intrathecal Routes of Administration for Adeno-Associated Viral Vectors in Large Animals
Christian Hinderer, Peter Bell, Nathan Katz, et al.
Human Molecular Genetics
|
September 22, 2017
Abnormal polyamine metabolism is unique to the neuropathic forms of MPS: potential for biomarker development and insight into pathogenesis
Christian Hinderer, Nathan Katz, Jean-Pierre Louboutin, et al.
Investigative Ophthalmology & Visual Science
|
July 19, 2012
RPGR-associated retinal degeneration in human X-linked RP and a murine model
Wei Chieh Huang, Alan F Wright, Alejandro J Roman, et al.
Science Advances
|
February 26, 2020
A mutation-independent CRISPR-Cas9-mediated gene targeting approach to treat a murine model of ornithine transcarbamylase deficiency
Lili Wang, Yang Yang, Camilo Breton, et al.
Nature Biotechnology
|
July 10, 2018
Meganuclease targeting of PCSK9 in macaque liver leads to stable reduction in serum cholesterol
Lili Wang, Jeff Smith, Camilo Breton, et al.
Molecular Therapy. Methods & Clinical Development
|
February 25, 2022
Prednisolone reduces the interferon response to AAV in cynomolgus macaques and may increase liver gene expression
Lili Wang, Claude C Warzecha, Alexander Kistner, et al.
Page
of 11