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Human Gene Therapy
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April 25, 2019
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys
Juliette Hordeaux, Christian Hinderer, Elizabeth L Buza, et al.
Human Gene Therapy
|
August 12, 2016
Delivery of an Adeno-Associated Virus Vector into Cerebrospinal Fluid Attenuates Central Nervous System Disease in Mucopolysaccharidosis Type II Mice
Christian Hinderer, Nathan Katz, Jean-Pierre Louboutin, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 27, 2005
No evidence for tumorigenesis of AAV vectors in a large-scale study in mice
Peter Bell, Lili Wang, Corinna Lebherz, et al.
Stem Cell Reports
|
September 23, 2014
Professional regulation: a potentially valuable tool in responding to "stem cell tourism"
Amy Zarzeczny, Timothy Caulfield, Ubaka Ogbogu, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 29, 2009
Systematic evaluation of AAV vectors for liver directed gene transfer in murine models
Lili Wang, Huan Wang, Peter Bell, et al.
Human Gene Therapy
|
May 16, 2009
Adeno-associated virus-mediated gene transfer to nonhuman primate liver can elicit destructive transgene-specific T cell responses
Guangping Gao, Qiang Wang, Roberto Calcedo, et al.
Human Gene Therapy. Clinical Development
|
January 30, 2019
A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease
Jenny A Greig, Jayme M L Nordin, Melanie K Smith, et al.
Molecular Therapy. Methods & Clinical Development
|
August 17, 2018
Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome
Jenny A Greig, Jayme M L Nordin, Christine Draper, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 2, 2019
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier
Juliette Hordeaux, Yuan Yuan, Peter M Clark, et al.
Nature Biotechnology
|
February 2, 2016
A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
Yang Yang, Lili Wang, Peter Bell, et al.
Page
of 11
Search research articles
Search
Showing results (61-70 of 105) with videos related to
Sort By:
Page
of 11
Human Gene Therapy
|
April 25, 2019
Safe and Sustained Expression of Human Iduronidase After Intrathecal Administration of Adeno-Associated Virus Serotype 9 in Infant Rhesus Monkeys
Juliette Hordeaux, Christian Hinderer, Elizabeth L Buza, et al.
Human Gene Therapy
|
August 12, 2016
Delivery of an Adeno-Associated Virus Vector into Cerebrospinal Fluid Attenuates Central Nervous System Disease in Mucopolysaccharidosis Type II Mice
Christian Hinderer, Nathan Katz, Jean-Pierre Louboutin, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
July 27, 2005
No evidence for tumorigenesis of AAV vectors in a large-scale study in mice
Peter Bell, Lili Wang, Corinna Lebherz, et al.
Stem Cell Reports
|
September 23, 2014
Professional regulation: a potentially valuable tool in responding to "stem cell tourism"
Amy Zarzeczny, Timothy Caulfield, Ubaka Ogbogu, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 29, 2009
Systematic evaluation of AAV vectors for liver directed gene transfer in murine models
Lili Wang, Huan Wang, Peter Bell, et al.
Human Gene Therapy
|
May 16, 2009
Adeno-associated virus-mediated gene transfer to nonhuman primate liver can elicit destructive transgene-specific T cell responses
Guangping Gao, Qiang Wang, Roberto Calcedo, et al.
Human Gene Therapy. Clinical Development
|
January 30, 2019
A Gene Therapy Approach to Improve Copper Metabolism and Prevent Liver Damage in a Mouse Model of Wilson Disease
Jenny A Greig, Jayme M L Nordin, Melanie K Smith, et al.
Molecular Therapy. Methods & Clinical Development
|
August 17, 2018
Determining the Minimally Effective Dose of a Clinical Candidate AAV Vector in a Mouse Model of Crigler-Najjar Syndrome
Jenny A Greig, Jayme M L Nordin, Christine Draper, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
March 2, 2019
The GPI-Linked Protein LY6A Drives AAV-PHP.B Transport across the Blood-Brain Barrier
Juliette Hordeaux, Yuan Yuan, Peter M Clark, et al.
Nature Biotechnology
|
February 2, 2016
A dual AAV system enables the Cas9-mediated correction of a metabolic liver disease in newborn mice
Yang Yang, Lili Wang, Peter Bell, et al.
Page
of 11