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Molecular Genetics and Metabolism
|
March 5, 2013
The Morquio A Clinical Assessment Program: baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects
Paul Harmatz, Karl Eugen Mengel, Roberto Giugliani, et al.
The Lancet. Neurology
|
December 15, 2023
Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study
Angela Schulz, Nicola Specchio, Emily de Los Reyes, et al.
Molecular Genetics and Metabolism
|
July 7, 2016
Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome
Christian J Hendriksz, Rossella Parini, Moeenaldeen D AlSayed, et al.
Molecular Genetics and Metabolism
|
January 14, 2015
Longitudinal analysis of endurance and respiratory function from a natural history study of Morquio A syndrome
Paul R Harmatz, Karl Eugen Mengel, Roberto Giugliani, et al.
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Search research articles
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Showing results (11-20 of 14) with videos related to
Sort By:
Page
of 2
You have reached the last page of results.
This site can display upto 14 results.
Molecular Genetics and Metabolism
|
March 5, 2013
The Morquio A Clinical Assessment Program: baseline results illustrating progressive, multisystemic clinical impairments in Morquio A subjects
Paul Harmatz, Karl Eugen Mengel, Roberto Giugliani, et al.
The Lancet. Neurology
|
December 15, 2023
Safety and efficacy of cerliponase alfa in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease): an open-label extension study
Angela Schulz, Nicola Specchio, Emily de Los Reyes, et al.
Molecular Genetics and Metabolism
|
July 7, 2016
Long-term endurance and safety of elosulfase alfa enzyme replacement therapy in patients with Morquio A syndrome
Christian J Hendriksz, Rossella Parini, Moeenaldeen D AlSayed, et al.
Molecular Genetics and Metabolism
|
January 14, 2015
Longitudinal analysis of endurance and respiratory function from a natural history study of Morquio A syndrome
Paul R Harmatz, Karl Eugen Mengel, Roberto Giugliani, et al.
Page
of 2