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Philippe Moullier

Showing results (81-90 of 92) with videos related to

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Molecular Therapy. Methods & Clinical Development|June 2, 2015
Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNAJean-Baptiste Dupont, Benoit Tournaire, Christophe Georger, et al.
Molecular Therapy. Methods & Clinical Development|May 2, 2020
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?Karim Bey, Johan Deniaud, Laurence Dubreil, et al.
Journal of Neuromuscular Diseases|November 19, 2016
Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe PhenotypeLaurent Servais, Marie Montus, Caroline Le Guiner, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 24, 2014
Liver-specific transcriptional modules identified by genome-wide in silico analysis enable efficient gene therapy in mice and non-human primatesMarinee K Chuah, Inge Petrus, Pieter De Bleser, et al.
Molecular Therapy. Methods & Clinical Development|February 8, 2024
Mannose-coupled AAV2: A second-generation AAV vector for increased retinal gene therapy efficiencyMathieu Mével, Virginie Pichard, Mohammed Bouzelha, et al.
Gene Therapy|February 2, 2022
Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and skeletal muscles in the DMD<sup>mdx</sup> rat modelAudrey Bourdon, Virginie François, Liwen Zhang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|December 9, 2010
Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromesN Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris, et al.
Science Translational Medicine|January 24, 2014
Gene therapy prolongs survival and restores function in murine and canine models of myotubular myopathyMartin K Childers, Romain Joubert, Karine Poulard, et al.
Nature Communications|July 26, 2017
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophyCaroline Le Guiner, Laurent Servais, Marie Montus, et al.
Human Gene Therapy|October 3, 2014
Manufacturing and characterization of a recombinant adeno-associated virus type 8 reference standard materialEduard Ayuso, Véronique Blouin, Martin Lock, et al.
Pageof 10

Showing results (81-90 of 92) with videos related to

Sort By:
Pageof 10
Molecular Therapy. Methods & Clinical Development|June 2, 2015
Short-lived recombinant adeno-associated virus transgene expression in dystrophic muscle is associated with oxidative damage to transgene mRNAJean-Baptiste Dupont, Benoit Tournaire, Christophe Georger, et al.
Molecular Therapy. Methods & Clinical Development|May 2, 2020
Intra-CSF AAV9 and AAVrh10 Administration in Nonhuman Primates: Promising Routes and Vectors for Which Neurological Diseases?Karim Bey, Johan Deniaud, Laurence Dubreil, et al.
Journal of Neuromuscular Diseases|November 19, 2016
Non-Ambulant Duchenne Patients Theoretically Treatable by Exon 53 Skipping have Severe PhenotypeLaurent Servais, Marie Montus, Caroline Le Guiner, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 24, 2014
Liver-specific transcriptional modules identified by genome-wide in silico analysis enable efficient gene therapy in mice and non-human primatesMarinee K Chuah, Inge Petrus, Pieter De Bleser, et al.
Molecular Therapy. Methods & Clinical Development|February 8, 2024
Mannose-coupled AAV2: A second-generation AAV vector for increased retinal gene therapy efficiencyMathieu Mével, Virginie Pichard, Mohammed Bouzelha, et al.
Gene Therapy|February 2, 2022
Evaluation of the dystrophin carboxy-terminal domain for micro-dystrophin gene therapy in cardiac and skeletal muscles in the DMD<sup>mdx</sup> rat modelAudrey Bourdon, Virginie François, Liwen Zhang, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|December 9, 2010
Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromesN Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris, et al.
Science Translational Medicine|January 24, 2014
Gene therapy prolongs survival and restores function in murine and canine models of myotubular myopathyMartin K Childers, Romain Joubert, Karine Poulard, et al.
Nature Communications|July 26, 2017
Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophyCaroline Le Guiner, Laurent Servais, Marie Montus, et al.
Human Gene Therapy|October 3, 2014
Manufacturing and characterization of a recombinant adeno-associated virus type 8 reference standard materialEduard Ayuso, Véronique Blouin, Martin Lock, et al.
Pageof 10