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Journal of Neurology, Neurosurgery, and Psychiatry
|
May 18, 2018
Acetazolamide can improve symptoms and signs in ion channel-related congenital myopathy
Emma Matthews, Louise Hartley, Richa Sud, et al.
European Journal of Human Genetics : EJHG
|
July 21, 2021
Biallelic P4HTM variants associated with HIDEA syndrome and mitochondrial respiratory chain complex I deficiency
Eleanor Hay, Louise C Wilson, Bethan Hoskins, et al.
Human Genome Variation
|
October 25, 2019
Novel missense variants in the <i>RNF213</i> gene from a European family with Moyamoya disease
Andrey N Gagunashvili, Louise Ocaka, Daniel Kelberman, et al.
The Journal of Pediatrics
|
July 1, 2017
Skeletal Muscle Channelopathies: Rare Disorders with Common Pediatric Symptoms
Emma Matthews, Arpana Silwal, Richa Sud, et al.
Brain Communications
|
November 30, 2023
Congenital myasthenic syndromes: a retrospective natural history study of respiratory outcomes in a single centre
Jordan Poulos, Martin Samuels, Jacqueline Palace, et al.
Brain : a Journal of Neurology
|
November 29, 2022
Early onset hereditary neuronopathies: an update on non-5q motor neuron diseases
Alberto A Zambon, Veronica Pini, Luca Bosco, et al.
BMJ Open
|
January 22, 2025
Spinal presentations in children with type 1 spinal muscular atrophy on nusinersen treatment across the SMA-REACH UK network: a retrospective national observational study
Lianne Abbott, Marion Main, Amy Wolfe, et al.
Pharmacoeconomics - Open
|
September 21, 2023
Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15
Marty Chaplin, Rebecca Bresnahan, Nigel Fleeman, et al.
Archives of Disease in Childhood
|
June 2, 2016
Vitamin D in corticosteroid-naïve and corticosteroid-treated Duchenne muscular dystrophy: what dose achieves optimal 25(OH) vitamin D levels?
Nahla Alshaikh, Andreas Brunklaus, Tracey Davis, et al.
Pharmacoeconomics - Open
|
December 5, 2023
Correction: Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15
Marty Chaplin, Rebecca Bresnahan, Nigel Fleeman, et al.
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Search research articles
Search
Showing results (11-20 of 59) with videos related to
Sort By:
Page
of 6
Journal of Neurology, Neurosurgery, and Psychiatry
|
May 18, 2018
Acetazolamide can improve symptoms and signs in ion channel-related congenital myopathy
Emma Matthews, Louise Hartley, Richa Sud, et al.
European Journal of Human Genetics : EJHG
|
July 21, 2021
Biallelic P4HTM variants associated with HIDEA syndrome and mitochondrial respiratory chain complex I deficiency
Eleanor Hay, Louise C Wilson, Bethan Hoskins, et al.
Human Genome Variation
|
October 25, 2019
Novel missense variants in the <i>RNF213</i> gene from a European family with Moyamoya disease
Andrey N Gagunashvili, Louise Ocaka, Daniel Kelberman, et al.
The Journal of Pediatrics
|
July 1, 2017
Skeletal Muscle Channelopathies: Rare Disorders with Common Pediatric Symptoms
Emma Matthews, Arpana Silwal, Richa Sud, et al.
Brain Communications
|
November 30, 2023
Congenital myasthenic syndromes: a retrospective natural history study of respiratory outcomes in a single centre
Jordan Poulos, Martin Samuels, Jacqueline Palace, et al.
Brain : a Journal of Neurology
|
November 29, 2022
Early onset hereditary neuronopathies: an update on non-5q motor neuron diseases
Alberto A Zambon, Veronica Pini, Luca Bosco, et al.
BMJ Open
|
January 22, 2025
Spinal presentations in children with type 1 spinal muscular atrophy on nusinersen treatment across the SMA-REACH UK network: a retrospective national observational study
Lianne Abbott, Marion Main, Amy Wolfe, et al.
Pharmacoeconomics - Open
|
September 21, 2023
Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15
Marty Chaplin, Rebecca Bresnahan, Nigel Fleeman, et al.
Archives of Disease in Childhood
|
June 2, 2016
Vitamin D in corticosteroid-naïve and corticosteroid-treated Duchenne muscular dystrophy: what dose achieves optimal 25(OH) vitamin D levels?
Nahla Alshaikh, Andreas Brunklaus, Tracey Davis, et al.
Pharmacoeconomics - Open
|
December 5, 2023
Correction: Onasemnogene Abeparvovec for Treating Pre-symptomatic Spinal Muscular Atrophy: An External Assessment Group Perspective of the Partial Review of NICE Highly Specialised Technology Evaluation 15
Marty Chaplin, Rebecca Bresnahan, Nigel Fleeman, et al.
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of 6