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Current Gene Therapy
|
October 8, 2009
Immunomodulatory gene therapy in lysosomal storage disorders
Dwight D Koeberl, Priya S Kishnani
Pediatric Endocrinology Reviews : PER
|
October 28, 2014
New therapeutic approaches for Pompe disease: enzyme replacement therapy and beyond
Priya S Kishnani, Alexandra A Beckemeyer
Pediatrics
|
November 23, 2017
Introduction to the Newborn Screening, Diagnosis, and Treatment for Pompe Disease Guidance Supplement
Priya S Kishnani, Wuh-Liang Hwu,
Annals of Translational Medicine
|
August 9, 2019
Liver depot gene therapy for Pompe disease
Priya S Kishnani, Dwight D Koeberl
American Journal of Medical Genetics. Part C, Seminars in Medical Genetics
|
October 19, 2006
Clinical manifestations of hematologic and oncologic disorders in patients with Down syndrome
Natalia Dixon, Priya S Kishnani, Sherri Zimmerman
Muscle & Nerve
|
January 17, 2012
How common is misdiagnosis in late-onset Pompe disease?
Lisa D Hobson-Webb, Priya S Kishnani
Molecular Genetics and Metabolism Reports
|
November 30, 2016
Right frontal lobe encephalomalacia in an adult propionic acidemia patient with neuropsychiatric manifestations
Pankaj Prasun, Lauren A Bailey, Priya S Kishnani
JCI Insight
|
October 20, 2022
Suppression of pullulanase-induced cytotoxic T cell response with a dual promoter in GSD IIIa mice
Jeong-A Lim, Priya S Kishnani, Baodong Sun
Human Molecular Genetics
|
June 23, 2019
Gene therapy for glycogen storage diseases
Priya S Kishnani, Baodong Sun, Dwight D Koeberl
American Journal of Medical Genetics. Part C, Seminars in Medical Genetics
|
January 19, 2012
The new era of Pompe disease: advances in the detection, understanding of the phenotypic spectrum, pathophysiology, and management
Priya S Kishnani, Alexandra A Beckemeyer, Nancy J Mendelsohn
Page
of 37
Search research articles
Search
Showing results (1-10 of 368) with videos related to
Sort By:
Page
of 37
Current Gene Therapy
|
October 8, 2009
Immunomodulatory gene therapy in lysosomal storage disorders
Dwight D Koeberl, Priya S Kishnani
Pediatric Endocrinology Reviews : PER
|
October 28, 2014
New therapeutic approaches for Pompe disease: enzyme replacement therapy and beyond
Priya S Kishnani, Alexandra A Beckemeyer
Pediatrics
|
November 23, 2017
Introduction to the Newborn Screening, Diagnosis, and Treatment for Pompe Disease Guidance Supplement
Priya S Kishnani, Wuh-Liang Hwu,
Annals of Translational Medicine
|
August 9, 2019
Liver depot gene therapy for Pompe disease
Priya S Kishnani, Dwight D Koeberl
American Journal of Medical Genetics. Part C, Seminars in Medical Genetics
|
October 19, 2006
Clinical manifestations of hematologic and oncologic disorders in patients with Down syndrome
Natalia Dixon, Priya S Kishnani, Sherri Zimmerman
Muscle & Nerve
|
January 17, 2012
How common is misdiagnosis in late-onset Pompe disease?
Lisa D Hobson-Webb, Priya S Kishnani
Molecular Genetics and Metabolism Reports
|
November 30, 2016
Right frontal lobe encephalomalacia in an adult propionic acidemia patient with neuropsychiatric manifestations
Pankaj Prasun, Lauren A Bailey, Priya S Kishnani
JCI Insight
|
October 20, 2022
Suppression of pullulanase-induced cytotoxic T cell response with a dual promoter in GSD IIIa mice
Jeong-A Lim, Priya S Kishnani, Baodong Sun
Human Molecular Genetics
|
June 23, 2019
Gene therapy for glycogen storage diseases
Priya S Kishnani, Baodong Sun, Dwight D Koeberl
American Journal of Medical Genetics. Part C, Seminars in Medical Genetics
|
January 19, 2012
The new era of Pompe disease: advances in the detection, understanding of the phenotypic spectrum, pathophysiology, and management
Priya S Kishnani, Alexandra A Beckemeyer, Nancy J Mendelsohn
Page
of 37