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R Giugliani

Showing results (121-130 of 164) with videos related to

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Clinical Genetics|September 27, 2014
p.L18P: a novel IDUA mutation that causes a distinct attenuated phenotype in mucopolysaccharidosis type I patientsG Pasqualim, M G Ribeiro, G G G da Fonseca, et al.
American Journal of Medical Genetics|July 1, 1993
DNA analysis of cystic fibrosis in Brazil by direct PCR amplification from Guthrie cardsS Raskin, J A Phillips, M R Krishnamani, et al.
Journal of Child Neurology|September 5, 2006
Diagnosis and molecular characterization of non-classic forms of Tay-Sachs disease in BrazilR Rozenberg, F Kok, M G Burin, et al.
Molecular Genetics and Metabolism Reports|March 1, 2017
Evaluation of impact of anti-idursulfase antibodies during long-term idursulfase enzyme replacement therapy in mucopolysaccharidosis II patientsR Giugliani, P Harmatz, S A Jones, et al.
Neurology|August 29, 2007
Brain MRI in mucopolysaccharidosis: effect of aging and correlation with biochemical findingsL Vedolin, I V D Schwartz, M Komlos, et al.
Journal of Inherited Metabolic Disease|May 26, 2004
CNS involvement in Fabry disease: clinical and imaging studies before and after 12 months of enzyme replacement therapyL Jardim, L Vedolin, I V D Schwartz, et al.
Journal of Inherited Metabolic Disease|September 15, 2006
Improvement of sympathetic skin responses under enzyme replacement therapy in Fabry diseaseL B Jardim, I Gomes, C B O Netto, et al.
Human Genetics|January 1, 1985
GM1 gangliosidosis: clinical and laboratory findings in eight familiesR Giugliani, J C Dutra, M L Pereira, et al.
Molecular Genetics and Metabolism|December 24, 2013
In vitro effect of genistein on DNA damage in leukocytes from mucopolysaccharidosis IVA patientsG W Negretto, M Deon, M Burin, et al.
Brazilian Journal of Medical and Biological Research = Revista Brasileira De Pesquisas Medicas E Biologicas|May 10, 2012
Severity score system for progressive myelopathy: development and validation of a new clinical scaleR M Castilhos, D Blank, C B O Netto, et al.
Pageof 17

Showing results (121-130 of 164) with videos related to

Sort By:
Pageof 17
Clinical Genetics|September 27, 2014
p.L18P: a novel IDUA mutation that causes a distinct attenuated phenotype in mucopolysaccharidosis type I patientsG Pasqualim, M G Ribeiro, G G G da Fonseca, et al.
American Journal of Medical Genetics|July 1, 1993
DNA analysis of cystic fibrosis in Brazil by direct PCR amplification from Guthrie cardsS Raskin, J A Phillips, M R Krishnamani, et al.
Journal of Child Neurology|September 5, 2006
Diagnosis and molecular characterization of non-classic forms of Tay-Sachs disease in BrazilR Rozenberg, F Kok, M G Burin, et al.
Molecular Genetics and Metabolism Reports|March 1, 2017
Evaluation of impact of anti-idursulfase antibodies during long-term idursulfase enzyme replacement therapy in mucopolysaccharidosis II patientsR Giugliani, P Harmatz, S A Jones, et al.
Neurology|August 29, 2007
Brain MRI in mucopolysaccharidosis: effect of aging and correlation with biochemical findingsL Vedolin, I V D Schwartz, M Komlos, et al.
Journal of Inherited Metabolic Disease|May 26, 2004
CNS involvement in Fabry disease: clinical and imaging studies before and after 12 months of enzyme replacement therapyL Jardim, L Vedolin, I V D Schwartz, et al.
Journal of Inherited Metabolic Disease|September 15, 2006
Improvement of sympathetic skin responses under enzyme replacement therapy in Fabry diseaseL B Jardim, I Gomes, C B O Netto, et al.
Human Genetics|January 1, 1985
GM1 gangliosidosis: clinical and laboratory findings in eight familiesR Giugliani, J C Dutra, M L Pereira, et al.
Molecular Genetics and Metabolism|December 24, 2013
In vitro effect of genistein on DNA damage in leukocytes from mucopolysaccharidosis IVA patientsG W Negretto, M Deon, M Burin, et al.
Brazilian Journal of Medical and Biological Research = Revista Brasileira De Pesquisas Medicas E Biologicas|May 10, 2012
Severity score system for progressive myelopathy: development and validation of a new clinical scaleR M Castilhos, D Blank, C B O Netto, et al.
Pageof 17