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Molecular Therapy. Methods & Clinical Development
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May 19, 2023
From Puppies to adults: <i>In vivo</i> editing of hepatocytes in a canine model of glycogen storage disease type Ia
Randy J Chandler
Molecular Therapy. Methods & Clinical Development
|
December 9, 2024
Determining recombinant AAV capsid extracellular and intracellular biodistribution by dual radioisotope labeling
Randy J Chandler
Proceedings of the National Academy of Sciences of the United States of America
|
September 21, 2019
Messenger RNA therapy as an option for treating metabolic disorders
Randy J Chandler
Journal of Visualized Experiments : Jove
|
June 3, 2024
Systemic Treatment for Postnatal, Juvenile, and Runted Adult Mice by Retrobulbar Sinus Injection
Darwin Romero, Randy J Chandler
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 3, 2011
A barrel of monkeys: scAAV8 gene therapy for hemophilia in nonhuman primates
Randy J Chandler, Charles P Venditti
Molecular Genetics and Metabolism
|
October 11, 2012
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)
Randy J Chandler, Charles P Venditti
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 29, 2009
Long-term rescue of a lethal murine model of methylmalonic acidemia using adeno-associated viral gene therapy
Randy J Chandler, Charles P Venditti
Human Gene Therapy
|
December 7, 2007
Adenovirus-mediated gene delivery rescues a neonatal lethal murine model of mut(0) methylmalonic acidemia
Randy J Chandler, Charles P Venditti
Journal of Inherited Metabolic Disease
|
August 2, 2023
Gene therapy for organic acidemias: Lessons learned from methylmalonic and propionic acidemia
Randy J Chandler, Charles P Venditti
Human Gene Therapy
|
July 16, 2019
Gene Therapy for Methylmalonic Acidemia: Past, Present, and Future
Randy J Chandler, Charles P Venditti
Page
of 5
Search research articles
Search
Showing results (1-10 of 47) with videos related to
Sort By:
Page
of 5
Molecular Therapy. Methods & Clinical Development
|
May 19, 2023
From Puppies to adults: <i>In vivo</i> editing of hepatocytes in a canine model of glycogen storage disease type Ia
Randy J Chandler
Molecular Therapy. Methods & Clinical Development
|
December 9, 2024
Determining recombinant AAV capsid extracellular and intracellular biodistribution by dual radioisotope labeling
Randy J Chandler
Proceedings of the National Academy of Sciences of the United States of America
|
September 21, 2019
Messenger RNA therapy as an option for treating metabolic disorders
Randy J Chandler
Journal of Visualized Experiments : Jove
|
June 3, 2024
Systemic Treatment for Postnatal, Juvenile, and Runted Adult Mice by Retrobulbar Sinus Injection
Darwin Romero, Randy J Chandler
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
May 3, 2011
A barrel of monkeys: scAAV8 gene therapy for hemophilia in nonhuman primates
Randy J Chandler, Charles P Venditti
Molecular Genetics and Metabolism
|
October 11, 2012
Pre-clinical efficacy and dosing of an AAV8 vector expressing human methylmalonyl-CoA mutase in a murine model of methylmalonic acidemia (MMA)
Randy J Chandler, Charles P Venditti
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
October 29, 2009
Long-term rescue of a lethal murine model of methylmalonic acidemia using adeno-associated viral gene therapy
Randy J Chandler, Charles P Venditti
Human Gene Therapy
|
December 7, 2007
Adenovirus-mediated gene delivery rescues a neonatal lethal murine model of mut(0) methylmalonic acidemia
Randy J Chandler, Charles P Venditti
Journal of Inherited Metabolic Disease
|
August 2, 2023
Gene therapy for organic acidemias: Lessons learned from methylmalonic and propionic acidemia
Randy J Chandler, Charles P Venditti
Human Gene Therapy
|
July 16, 2019
Gene Therapy for Methylmalonic Acidemia: Past, Present, and Future
Randy J Chandler, Charles P Venditti
Page
of 5