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Annals of Neurology
|
August 3, 2024
Solving the Etiology of Developmental and Epileptic Encephalopathy with Spike-Wave Activation in Sleep (D/EE-SWAS)
Sindhu Viswanathan, Karen L Oliver, Brigid M Regan, et al.
American Journal of Medical Genetics. Part A
|
June 6, 2020
Activating variants in PDGFRB result in a spectrum of disorders responsive to imatinib monotherapy
Tara L Wenger, Randall A Bly, Natalie Wu, et al.
Neurology
|
August 28, 2019
Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function
Eric P Hoffman, Benjamin D Schwartz, Laurel J Mengle-Gaw, et al.
Nature Genetics
|
May 28, 2013
Targeted resequencing in epileptic encephalopathies identifies de novo mutations in CHD2 and SYNGAP1
Gemma L Carvill, Sinéad B Heavin, Simone C Yendle, et al.
Pharmacological Research
|
September 17, 2018
Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
Laurie S Conklin, Jesse M Damsker, Eric P Hoffman, et al.
Neurology. Genetics
|
February 12, 2020
Clinical spectrum of POLR3-related leukodystrophy caused by biallelic <i>POLR1C</i> pathogenic variants
Laurence Gauquelin, Ferdy K Cayami, László Sztriha, et al.
American Journal of Human Genetics
|
December 5, 2017
A Recurrent De Novo Nonsense Variant in ZSWIM6 Results in Severe Intellectual Disability without Frontonasal or Limb Malformations
Elizabeth E Palmer, Raman Kumar, Christopher T Gordon, et al.
Human Mutation
|
June 18, 2019
Deleterious de novo variants of X-linked ZC4H2 in females cause a variable phenotype with neurogenic arthrogryposis multiplex congenita
Suzanna G M Frints, Friederike Hennig, Roberto Colombo, et al.
BMJ Open
|
April 22, 2025
TRANSCENDENT (Transforming Research by Assessing Neuroinformatics across the Spectrum of Concussion by Embedding iNterdisciplinary Data-collection to Enable Novel Treatments): protocol for a prospective observational cohort study of concussion patients with embedded comparative effectiveness research within a network of learning health system concussion clinics in Canada
Roger Zemek, Lisa M Albrecht, Sharon Johnston, et al.
American Journal of Human Genetics
|
April 30, 2013
ZC4H2 mutations are associated with arthrogryposis multiplex congenita and intellectual disability through impairment of central and peripheral synaptic plasticity
Hiromi Hirata, Indrajit Nanda, Anne van Riesen, et al.
Page
of 17
Search research articles
Search
Showing results (151-160 of 163) with videos related to
Sort By:
Page
of 17
Annals of Neurology
|
August 3, 2024
Solving the Etiology of Developmental and Epileptic Encephalopathy with Spike-Wave Activation in Sleep (D/EE-SWAS)
Sindhu Viswanathan, Karen L Oliver, Brigid M Regan, et al.
American Journal of Medical Genetics. Part A
|
June 6, 2020
Activating variants in PDGFRB result in a spectrum of disorders responsive to imatinib monotherapy
Tara L Wenger, Randall A Bly, Natalie Wu, et al.
Neurology
|
August 28, 2019
Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function
Eric P Hoffman, Benjamin D Schwartz, Laurel J Mengle-Gaw, et al.
Nature Genetics
|
May 28, 2013
Targeted resequencing in epileptic encephalopathies identifies de novo mutations in CHD2 and SYNGAP1
Gemma L Carvill, Sinéad B Heavin, Simone C Yendle, et al.
Pharmacological Research
|
September 17, 2018
Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug
Laurie S Conklin, Jesse M Damsker, Eric P Hoffman, et al.
Neurology. Genetics
|
February 12, 2020
Clinical spectrum of POLR3-related leukodystrophy caused by biallelic <i>POLR1C</i> pathogenic variants
Laurence Gauquelin, Ferdy K Cayami, László Sztriha, et al.
American Journal of Human Genetics
|
December 5, 2017
A Recurrent De Novo Nonsense Variant in ZSWIM6 Results in Severe Intellectual Disability without Frontonasal or Limb Malformations
Elizabeth E Palmer, Raman Kumar, Christopher T Gordon, et al.
Human Mutation
|
June 18, 2019
Deleterious de novo variants of X-linked ZC4H2 in females cause a variable phenotype with neurogenic arthrogryposis multiplex congenita
Suzanna G M Frints, Friederike Hennig, Roberto Colombo, et al.
BMJ Open
|
April 22, 2025
TRANSCENDENT (Transforming Research by Assessing Neuroinformatics across the Spectrum of Concussion by Embedding iNterdisciplinary Data-collection to Enable Novel Treatments): protocol for a prospective observational cohort study of concussion patients with embedded comparative effectiveness research within a network of learning health system concussion clinics in Canada
Roger Zemek, Lisa M Albrecht, Sharon Johnston, et al.
American Journal of Human Genetics
|
April 30, 2013
ZC4H2 mutations are associated with arthrogryposis multiplex congenita and intellectual disability through impairment of central and peripheral synaptic plasticity
Hiromi Hirata, Indrajit Nanda, Anne van Riesen, et al.
Page
of 17