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American Journal of Human Genetics|October 6, 2018
Mutations in KCNK4 that Affect Gating Cause a Recognizable Neurodevelopmental SyndromeChristiane K Bauer, Paolo Calligari, Francesca Clementina Radio, et al.
Brain : a Journal of Neurology|February 3, 2009
Clinical, histological and genetic characterization of reducing body myopathy caused by mutations in FHL1Joachim Schessl, Ana L Taratuto, Caroline Sewry, et al.
American Journal of Medical Genetics. Part A|April 5, 2014
Interstitial 22q13 deletions not involving SHANK3 gene: a new contiguous gene syndromeVittoria Disciglio, Caterina Lo Rizzo, Maria Antonietta Mencarelli, et al.
European Journal of Human Genetics : EJHG|October 11, 2024
Pathogenic cryptic variants detectable through exome data reanalysis significantly increase the diagnostic yield in Joubert syndromeFulvio D'Abrusco, Valentina Serpieri, Cecilia Maria Taccagni, et al.
Journal of Medical Genetics|February 14, 2023
Recurrent, founder and hypomorphic variants contribute to the genetic landscape of Joubert syndromeValentina Serpieri, Giulia Mortarini, Hailey Loucks, et al.
Frontiers in Neurology|June 27, 2022
The Clinical Impact of Methotrexate-Induced Stroke-Like Neurotoxicity in Paediatric Departments: An Italian Multi-Centre Case-SeriesAndrea Santangelo, Emanuele Bartolini, Giulia Nuzzi, et al.
Journal of Neurology|November 9, 2013
"I have got something positive out of this situation": psychological benefits of caregiving in relatives of young people with muscular dystrophyLorenza Magliano, Melania Patalano, Alessandra Sagliocchi, et al.
Neuromuscular Disorders : NMD|March 7, 2017
Diagnosis of Duchenne Muscular Dystrophy in Italy in the last decade: Critical issues and areas for improvementsAdele D'Amico, Michela Catteruccia, Giovanni Baranello, et al.
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