Search research articles
Contact Us
Filters
Showing results (91-100 of 111) with videos related to
Page
of 12
Sort By:
European Journal of Pediatrics
|
January 20, 2022
Body mass index in type 2 spinal muscular atrophy: a longitudinal study
Gloria Ferrantini, Giorgia Coratti, Roberta Onesimo, et al.
European Journal of Pediatrics
|
August 29, 2024
Prognostic factors for tube feeding in type I SMA patients treated with disease-modifying therapies: a cohort study
Marika Pane, Giulia Stanca, Giorgia Coratti, et al.
Clinical Genetics
|
July 17, 2023
Congenital heart defects in CTNNB1 syndrome: Raising clinical awareness
Lorenzo Sinibaldi, Giacomo Garone, Alessandra Mandarino, et al.
European Journal of Human Genetics : EJHG
|
February 26, 2025
Expanding the mutational spectrum of ReNU syndrome: insights into 5' Stem-loop variants
Alessandro Bruselles, Cecilia Mancini, Luigi Chiriatti, et al.
Human Molecular Genetics
|
March 29, 2022
Expanding the molecular spectrum of pathogenic SHOC2 variants underlying Mazzanti syndrome
Marialetizia Motta, Maja Solman, Adeline A Bonnard, et al.
Orphanet Journal of Rare Diseases
|
March 16, 2023
Lifetime impact of achondroplasia study in Europe (LIAISE): findings from a multinational observational study
Mohamad Maghnie, Oliver Semler, Encarna Guillen-Navarro, et al.
European Journal of Pediatrics
|
April 18, 2024
Early neurological signs in infants identified through neonatal screening for SMA: do they predict outcome?
Marika Pane, Giulia Stanca, Chiara Ticci, et al.
Eclinicalmedicine
|
May 17, 2023
Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapies
Marika Pane, Beatrice Berti, Anna Capasso, et al.
The Pediatric Infectious Disease Journal
|
November 11, 2025
Necrotizing Pneumonia in Critically Ill Infants and Children: Predictive Factors for Critical Care Requirement
Marco Piastra, Ivonne Portaccio, Geremia Zito Marinosci, et al.
American Journal of Human Genetics
|
November 13, 2020
De Novo VPS4A Mutations Cause Multisystem Disease with Abnormal Neurodevelopment
Catherine Rodger, Elisabetta Flex, Rachel J Allison, et al.
Page
of 12
Search research articles
Search
Showing results (91-100 of 111) with videos related to
Sort By:
Page
of 12
European Journal of Pediatrics
|
January 20, 2022
Body mass index in type 2 spinal muscular atrophy: a longitudinal study
Gloria Ferrantini, Giorgia Coratti, Roberta Onesimo, et al.
European Journal of Pediatrics
|
August 29, 2024
Prognostic factors for tube feeding in type I SMA patients treated with disease-modifying therapies: a cohort study
Marika Pane, Giulia Stanca, Giorgia Coratti, et al.
Clinical Genetics
|
July 17, 2023
Congenital heart defects in CTNNB1 syndrome: Raising clinical awareness
Lorenzo Sinibaldi, Giacomo Garone, Alessandra Mandarino, et al.
European Journal of Human Genetics : EJHG
|
February 26, 2025
Expanding the mutational spectrum of ReNU syndrome: insights into 5' Stem-loop variants
Alessandro Bruselles, Cecilia Mancini, Luigi Chiriatti, et al.
Human Molecular Genetics
|
March 29, 2022
Expanding the molecular spectrum of pathogenic SHOC2 variants underlying Mazzanti syndrome
Marialetizia Motta, Maja Solman, Adeline A Bonnard, et al.
Orphanet Journal of Rare Diseases
|
March 16, 2023
Lifetime impact of achondroplasia study in Europe (LIAISE): findings from a multinational observational study
Mohamad Maghnie, Oliver Semler, Encarna Guillen-Navarro, et al.
European Journal of Pediatrics
|
April 18, 2024
Early neurological signs in infants identified through neonatal screening for SMA: do they predict outcome?
Marika Pane, Giulia Stanca, Chiara Ticci, et al.
Eclinicalmedicine
|
May 17, 2023
Onasemnogene abeparvovec in spinal muscular atrophy: predictors of efficacy and safety in naïve patients with spinal muscular atrophy and following switch from other therapies
Marika Pane, Beatrice Berti, Anna Capasso, et al.
The Pediatric Infectious Disease Journal
|
November 11, 2025
Necrotizing Pneumonia in Critically Ill Infants and Children: Predictive Factors for Critical Care Requirement
Marco Piastra, Ivonne Portaccio, Geremia Zito Marinosci, et al.
American Journal of Human Genetics
|
November 13, 2020
De Novo VPS4A Mutations Cause Multisystem Disease with Abnormal Neurodevelopment
Catherine Rodger, Elisabetta Flex, Rachel J Allison, et al.
Page
of 12