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Wires Mechanisms of Disease
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November 3, 2021
Disruption of morphogenic and growth pathways in lysosomal storage diseases
Thiago Corrêa, Bruno C Feltes, Roberto Giugliani, et al.
Molecular Genetics and Metabolism
|
January 22, 2025
Exploratory metabolomic profiling of plasma and urine in patients with mucopolysaccharidosis type II (Hunter syndrome): A pilot study
Asma Farjallah, Bruno Maranda, Roberto Giugliani, et al.
Metabolomics : Official Journal of the Metabolomic Society
|
March 2, 2025
Identification of gangliosides and ceramides as biomarkers for mucopolysaccharidosis type II (hunter syndrome) through untargeted lipidomic analysis
Asma Farjallah, Bruno Maranda, Roberto Giugliani, et al.
Drugs
|
October 12, 2025
Current and Emerging Treatments for Acid Sphingomyelinase Deficiency
Tamires Silva Alves, Ana Luíza Fonseca Siqueira, Roberto Giugliani
Emerging Infectious Diseases
|
June 23, 2004
Newborn screening for congenital infectious diseases
Eurico Camargo Neto, Rosélia Rubin, Jacqueline Schulte, et al.
Journal of Inherited Metabolic Disease
|
January 7, 2026
From Molecule to Meaning: Neuronopathic Biomarkers and Clinical Relevance in GM1
Krista Casazza, Roberto Giugliani, Debra S Regier, et al.
Orphanet Journal of Rare Diseases
|
April 21, 2020
Assessing the impact of the five senses on quality of life in mucopolysaccharidoses
Roberto Giugliani, Paul Harmatz, Shuan-Pei Lin, et al.
Genetics and Molecular Biology
|
May 28, 2019
Effects of gene therapy on cardiovascular symptoms of lysosomal storage diseases
Edina Poletto, Gabriela Pasqualim, Roberto Giugliani, et al.
Orphanet Journal of Rare Diseases
|
November 19, 2020
Estimated prevalence of mucopolysaccharidoses from population-based exomes and genomes
Pâmella Borges, Gabriela Pasqualim, Roberto Giugliani, et al.
Molecular Genetics and Metabolism Reports
|
May 19, 2017
Birth weight in patients with mucopolysaccharidosis type II: Data from the Hunter Outcome Survey (HOS)
Olaf Bodamer, Maurizio Scarpa, Christina Hung, et al.
Page
of 49
Search research articles
Search
Showing results (21-30 of 482) with videos related to
Sort By:
Page
of 49
Wires Mechanisms of Disease
|
November 3, 2021
Disruption of morphogenic and growth pathways in lysosomal storage diseases
Thiago Corrêa, Bruno C Feltes, Roberto Giugliani, et al.
Molecular Genetics and Metabolism
|
January 22, 2025
Exploratory metabolomic profiling of plasma and urine in patients with mucopolysaccharidosis type II (Hunter syndrome): A pilot study
Asma Farjallah, Bruno Maranda, Roberto Giugliani, et al.
Metabolomics : Official Journal of the Metabolomic Society
|
March 2, 2025
Identification of gangliosides and ceramides as biomarkers for mucopolysaccharidosis type II (hunter syndrome) through untargeted lipidomic analysis
Asma Farjallah, Bruno Maranda, Roberto Giugliani, et al.
Drugs
|
October 12, 2025
Current and Emerging Treatments for Acid Sphingomyelinase Deficiency
Tamires Silva Alves, Ana Luíza Fonseca Siqueira, Roberto Giugliani
Emerging Infectious Diseases
|
June 23, 2004
Newborn screening for congenital infectious diseases
Eurico Camargo Neto, Rosélia Rubin, Jacqueline Schulte, et al.
Journal of Inherited Metabolic Disease
|
January 7, 2026
From Molecule to Meaning: Neuronopathic Biomarkers and Clinical Relevance in GM1
Krista Casazza, Roberto Giugliani, Debra S Regier, et al.
Orphanet Journal of Rare Diseases
|
April 21, 2020
Assessing the impact of the five senses on quality of life in mucopolysaccharidoses
Roberto Giugliani, Paul Harmatz, Shuan-Pei Lin, et al.
Genetics and Molecular Biology
|
May 28, 2019
Effects of gene therapy on cardiovascular symptoms of lysosomal storage diseases
Edina Poletto, Gabriela Pasqualim, Roberto Giugliani, et al.
Orphanet Journal of Rare Diseases
|
November 19, 2020
Estimated prevalence of mucopolysaccharidoses from population-based exomes and genomes
Pâmella Borges, Gabriela Pasqualim, Roberto Giugliani, et al.
Molecular Genetics and Metabolism Reports
|
May 19, 2017
Birth weight in patients with mucopolysaccharidosis type II: Data from the Hunter Outcome Survey (HOS)
Olaf Bodamer, Maurizio Scarpa, Christina Hung, et al.
Page
of 49