Search research articles
Contact Us
Filters
Showing results (11-20 of 53) with videos related to
Page
of 6
Sort By:
Molecular Genetics and Metabolism
|
December 17, 2008
A new surrogate marker for CNS pathology in Niemann-Pick disease type C?
Frances M Platt, Robin H Lachmann
Journal of Inherited Metabolic Disease
|
April 4, 2022
Lost in translation-Challenges in drug development for inherited metabolic diseases
Robin H Lachmann, Marc C Patterson, Sandra Sirrs
Ophthalmology
|
April 5, 2011
Latency vs saccadic parameters in lysosomal trials
Jonathan C P Roos, Robin H Lachmann, Roger H Carpenter, et al.
Journal of Inherited Metabolic Disease
|
August 17, 2013
Cognitive dysfunction and depression in Fabry disease: a systematic review
Fay E Bolsover, Elaine Murphy, Lisa Cipolotti, et al.
The Biochemical Journal
|
September 18, 2007
Glucosylated free oligosaccharides are biomarkers of endoplasmic- reticulum alpha-glucosidase inhibition
Dominic S Alonzi, David C A Neville, Robin H Lachmann, et al.
Journal of Inherited Metabolic Disease
|
February 4, 2011
Dietary treatment of phenylketonuria: the effect of phenylalanine on reaction time
Charlotte Dawson, Elaine Murphy, Charlé Maritz, et al.
Journal of Inherited Metabolic Disease
|
September 28, 2011
Pregnancy and its management in women with GSD type III - a single centre experience
Radha Ramachandran, Yehani Wedatilake, Caroline Coats, et al.
Journal of Inherited Metabolic Disease
|
January 29, 2019
The neurological and psychological phenotype of adult patients with early-treated phenylketonuria: A systematic review
Alessandro P Burlina, Robin H Lachmann, Renzo Manara, et al.
Orphanet Journal of Rare Diseases
|
April 25, 2023
Olipudase alfa enzyme replacement therapy for acid sphingomyelinase deficiency (ASMD): sustained improvements in clinical outcomes after 6.5 years of treatment in adults
Robin H Lachmann, George A Diaz, Melissa P Wasserstein, et al.
The New England Journal of Medicine
|
March 28, 2008
An adult with type 2 citrullinemia presenting in Europe
Giuseppe Fiermonte, Derek Soon, Abhijit Chaudhuri, et al.
Page
of 6
Search research articles
Search
Showing results (11-20 of 53) with videos related to
Sort By:
Page
of 6
Molecular Genetics and Metabolism
|
December 17, 2008
A new surrogate marker for CNS pathology in Niemann-Pick disease type C?
Frances M Platt, Robin H Lachmann
Journal of Inherited Metabolic Disease
|
April 4, 2022
Lost in translation-Challenges in drug development for inherited metabolic diseases
Robin H Lachmann, Marc C Patterson, Sandra Sirrs
Ophthalmology
|
April 5, 2011
Latency vs saccadic parameters in lysosomal trials
Jonathan C P Roos, Robin H Lachmann, Roger H Carpenter, et al.
Journal of Inherited Metabolic Disease
|
August 17, 2013
Cognitive dysfunction and depression in Fabry disease: a systematic review
Fay E Bolsover, Elaine Murphy, Lisa Cipolotti, et al.
The Biochemical Journal
|
September 18, 2007
Glucosylated free oligosaccharides are biomarkers of endoplasmic- reticulum alpha-glucosidase inhibition
Dominic S Alonzi, David C A Neville, Robin H Lachmann, et al.
Journal of Inherited Metabolic Disease
|
February 4, 2011
Dietary treatment of phenylketonuria: the effect of phenylalanine on reaction time
Charlotte Dawson, Elaine Murphy, Charlé Maritz, et al.
Journal of Inherited Metabolic Disease
|
September 28, 2011
Pregnancy and its management in women with GSD type III - a single centre experience
Radha Ramachandran, Yehani Wedatilake, Caroline Coats, et al.
Journal of Inherited Metabolic Disease
|
January 29, 2019
The neurological and psychological phenotype of adult patients with early-treated phenylketonuria: A systematic review
Alessandro P Burlina, Robin H Lachmann, Renzo Manara, et al.
Orphanet Journal of Rare Diseases
|
April 25, 2023
Olipudase alfa enzyme replacement therapy for acid sphingomyelinase deficiency (ASMD): sustained improvements in clinical outcomes after 6.5 years of treatment in adults
Robin H Lachmann, George A Diaz, Melissa P Wasserstein, et al.
The New England Journal of Medicine
|
March 28, 2008
An adult with type 2 citrullinemia presenting in Europe
Giuseppe Fiermonte, Derek Soon, Abhijit Chaudhuri, et al.
Page
of 6