Search research articles
Contact Us
Filters
Showing results (151-160 of 175) with videos related to
Page
of 18
Sort By:
Investigative Ophthalmology & Visual Science
|
February 11, 2015
Advancing therapeutic strategies for inherited retinal degeneration: recommendations from the Monaciano Symposium
Debra A Thompson, Robin R Ali, Eyal Banin, et al.
Nature Medicine
|
February 24, 2006
Effective gene therapy with nonintegrating lentiviral vectors
Rafael J Yáñez-Muñoz, Kamaljit S Balaggan, Angus MacNeil, et al.
Stem Cell Reports
|
May 30, 2017
Differentiation and Transplantation of Embryonic Stem Cell-Derived Cone Photoreceptors into a Mouse Model of End-Stage Retinal Degeneration
Kamil Kruczek, Anai Gonzalez-Cordero, Debbie Goh, et al.
Human Gene Therapy
|
March 28, 2018
Assessment of AAV Vector Tropisms for Mouse and Human Pluripotent Stem Cell-Derived RPE and Photoreceptor Cells
Anai Gonzalez-Cordero, Debbie Goh, Kamil Kruczek, et al.
The New England Journal of Medicine
|
April 29, 2008
Effect of gene therapy on visual function in Leber's congenital amaurosis
James W B Bainbridge, Alexander J Smith, Susie S Barker, et al.
Human Molecular Genetics
|
January 10, 2017
Rescue of mutant rhodopsin traffic by metformin-induced AMPK activation accelerates photoreceptor degeneration
Dimitra Athanasiou, Monica Aguila, Chikwado A Opefi, et al.
Plos One
|
March 14, 2012
Leber congenital amaurosis associated with AIPL1: challenges in ascribing disease causation, clinical findings, and implications for gene therapy
Mei Hong Tan, Donna S Mackay, Jill Cowing, et al.
Human Gene Therapy
|
December 29, 2025
Brain-Directed AAV Gene Therapy Rescues a Mouse Model of the CLN5 Form of Neuronal Ceroid Lipofuscinosis Disease and Normalizes a Blood Plasma Biomarker of Neurodegeneration
Wenfei Liu, Amy F Geard, Giulia Massaro, et al.
Lancet (London, England)
|
December 22, 2004
Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector
H Bobby Gaspar, Kathryn L Parsley, Steven Howe, et al.
Cell Reports
|
April 21, 2021
Restoration of visual function in advanced disease after transplantation of purified human pluripotent stem cell-derived cone photoreceptors
Joana Ribeiro, Christopher A Procyk, Emma L West, et al.
Page
of 18
Search research articles
Search
Showing results (151-160 of 175) with videos related to
Sort By:
Page
of 18
Investigative Ophthalmology & Visual Science
|
February 11, 2015
Advancing therapeutic strategies for inherited retinal degeneration: recommendations from the Monaciano Symposium
Debra A Thompson, Robin R Ali, Eyal Banin, et al.
Nature Medicine
|
February 24, 2006
Effective gene therapy with nonintegrating lentiviral vectors
Rafael J Yáñez-Muñoz, Kamaljit S Balaggan, Angus MacNeil, et al.
Stem Cell Reports
|
May 30, 2017
Differentiation and Transplantation of Embryonic Stem Cell-Derived Cone Photoreceptors into a Mouse Model of End-Stage Retinal Degeneration
Kamil Kruczek, Anai Gonzalez-Cordero, Debbie Goh, et al.
Human Gene Therapy
|
March 28, 2018
Assessment of AAV Vector Tropisms for Mouse and Human Pluripotent Stem Cell-Derived RPE and Photoreceptor Cells
Anai Gonzalez-Cordero, Debbie Goh, Kamil Kruczek, et al.
The New England Journal of Medicine
|
April 29, 2008
Effect of gene therapy on visual function in Leber's congenital amaurosis
James W B Bainbridge, Alexander J Smith, Susie S Barker, et al.
Human Molecular Genetics
|
January 10, 2017
Rescue of mutant rhodopsin traffic by metformin-induced AMPK activation accelerates photoreceptor degeneration
Dimitra Athanasiou, Monica Aguila, Chikwado A Opefi, et al.
Plos One
|
March 14, 2012
Leber congenital amaurosis associated with AIPL1: challenges in ascribing disease causation, clinical findings, and implications for gene therapy
Mei Hong Tan, Donna S Mackay, Jill Cowing, et al.
Human Gene Therapy
|
December 29, 2025
Brain-Directed AAV Gene Therapy Rescues a Mouse Model of the CLN5 Form of Neuronal Ceroid Lipofuscinosis Disease and Normalizes a Blood Plasma Biomarker of Neurodegeneration
Wenfei Liu, Amy F Geard, Giulia Massaro, et al.
Lancet (London, England)
|
December 22, 2004
Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector
H Bobby Gaspar, Kathryn L Parsley, Steven Howe, et al.
Cell Reports
|
April 21, 2021
Restoration of visual function in advanced disease after transplantation of purified human pluripotent stem cell-derived cone photoreceptors
Joana Ribeiro, Christopher A Procyk, Emma L West, et al.
Page
of 18