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Robin R Ali

Showing results (161-170 of 175) with videos related to

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Stem Cells (Dayton, Ohio)|May 4, 2026
Transplantation of human stem cell-derived cone photoreceptors partially restores vision in aged rd1 mice with advanced retinal degenerationChristopher A Procyk, Anna Melati, Menahil Tariq, et al.
Blood|July 3, 2004
Permanent phenotypic correction of hemophilia B in immunocompetent mice by prenatal gene therapySimon N Waddington, Megha S Nivsarkar, Ajay R Mistry, et al.
Ophthalmology|June 10, 2018
Transplantation of Human Embryonic Stem Cell-Derived Retinal Pigment Epithelial Cells in Macular DegenerationManjit S Mehat, Venki Sundaram, Caterina Ripamonti, et al.
Stem Cell Reports|August 29, 2017
Recapitulation of Human Retinal Development from Human Pluripotent Stem Cells Generates Transplantable Populations of Cone PhotoreceptorsAnai Gonzalez-Cordero, Kamil Kruczek, Arifa Naeem, et al.
American Journal of Ophthalmology|May 12, 2023
First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated AchromatopsiaMichel Michaelides, Nashila Hirji, Sui Chien Wong, et al.
Lancet (London, England)|February 22, 2025
Gene therapy in children with AIPL1-associated severe retinal dystrophy: an open-label, first-in-human interventional studyMichel Michaelides, Yannik Laich, Sui Chien Wong, et al.
Stem Cell Reports|January 9, 2018
Transplanted Donor- or Stem Cell-Derived Cone Photoreceptors Can Both Integrate and Undergo Material Transfer in an Environment-Dependent MannerPaul V Waldron, Fabiana Di Marco, Kamil Kruczek, et al.
Nature Medicine|December 8, 2009
Comprehensive genomic access to vector integration in clinical gene therapyRichard Gabriel, Ralph Eckenberg, Anna Paruzynski, et al.
American Journal of Ophthalmology|June 13, 2024
Phase 1/2 AAV5-hRKp.RPGR (Botaretigene Sparoparvovec) Gene Therapy: Safety and Efficacy in RPGR-Associated X-Linked Retinitis PigmentosaMichel Michaelides, Cagri G Besirli, Yesa Yang, et al.
Nature Communications|April 11, 2024
PRPF8-mediated dysregulation of hBrr2 helicase disrupts human spliceosome kinetics and 5´-splice-site selection causing tissue-specific defectsRobert Atkinson, Maria Georgiou, Chunbo Yang, et al.
Pageof 18

Showing results (161-170 of 175) with videos related to

Sort By:
Pageof 18
Stem Cells (Dayton, Ohio)|May 4, 2026
Transplantation of human stem cell-derived cone photoreceptors partially restores vision in aged rd1 mice with advanced retinal degenerationChristopher A Procyk, Anna Melati, Menahil Tariq, et al.
Blood|July 3, 2004
Permanent phenotypic correction of hemophilia B in immunocompetent mice by prenatal gene therapySimon N Waddington, Megha S Nivsarkar, Ajay R Mistry, et al.
Ophthalmology|June 10, 2018
Transplantation of Human Embryonic Stem Cell-Derived Retinal Pigment Epithelial Cells in Macular DegenerationManjit S Mehat, Venki Sundaram, Caterina Ripamonti, et al.
Stem Cell Reports|August 29, 2017
Recapitulation of Human Retinal Development from Human Pluripotent Stem Cells Generates Transplantable Populations of Cone PhotoreceptorsAnai Gonzalez-Cordero, Kamil Kruczek, Arifa Naeem, et al.
American Journal of Ophthalmology|May 12, 2023
First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated AchromatopsiaMichel Michaelides, Nashila Hirji, Sui Chien Wong, et al.
Lancet (London, England)|February 22, 2025
Gene therapy in children with AIPL1-associated severe retinal dystrophy: an open-label, first-in-human interventional studyMichel Michaelides, Yannik Laich, Sui Chien Wong, et al.
Stem Cell Reports|January 9, 2018
Transplanted Donor- or Stem Cell-Derived Cone Photoreceptors Can Both Integrate and Undergo Material Transfer in an Environment-Dependent MannerPaul V Waldron, Fabiana Di Marco, Kamil Kruczek, et al.
Nature Medicine|December 8, 2009
Comprehensive genomic access to vector integration in clinical gene therapyRichard Gabriel, Ralph Eckenberg, Anna Paruzynski, et al.
American Journal of Ophthalmology|June 13, 2024
Phase 1/2 AAV5-hRKp.RPGR (Botaretigene Sparoparvovec) Gene Therapy: Safety and Efficacy in RPGR-Associated X-Linked Retinitis PigmentosaMichel Michaelides, Cagri G Besirli, Yesa Yang, et al.
Nature Communications|April 11, 2024
PRPF8-mediated dysregulation of hBrr2 helicase disrupts human spliceosome kinetics and 5´-splice-site selection causing tissue-specific defectsRobert Atkinson, Maria Georgiou, Chunbo Yang, et al.
Pageof 18