Showing results (21-30 of 47) with videos related to

Sort By:
Pageof 5
The Journal of Gene Medicine|June 20, 2012
Assessment of the nuclear pore dilating agent trans-cyclohexane-1,2-diol in differentiated airway epitheliumUta Griesenbach, Katherine M Wilson, Raymond Farley, et al.
Respiratory Research|September 25, 2008
Role of viral hemagglutinin glycosylation in anti-influenza activities of recombinant surfactant protein DKevan L Hartshorn, Richard Webby, Mitchell R White, et al.
The Journal of Gene Medicine|January 13, 2004
Partial correction of the alpha-galactosidase A deficiency and reduction of glycolipid storage in Fabry mice using synthetic vectorsMalgorzata Przybylska, I-Huan Wu, Hongmei Zhao, et al.
Biomaterials|January 21, 2009
The role of doxorubicin in non-viral gene transfer in the lungUta Griesenbach, Cuixiang Meng, Raymond Farley, et al.
Journal of Inherited Metabolic Disease|March 26, 2010
Improved management of lysosomal glucosylceramide levels in a mouse model of type 1 Gaucher disease using enzyme and substrate reduction therapyJohn Marshall, Kerry Anne McEachern, Wei-Lien Chuang, et al.
Molecular Therapy. Nucleic Acids|October 29, 2014
Antisense Oligonucleotide-mediated Suppression of Muscle Glycogen Synthase 1 Synthesis as an Approach for Substrate Reduction Therapy of Pompe DiseaseNicholas P Clayton, Carol A Nelson, Timothy Weeden, et al.
Plos One|December 3, 2010
Substrate reduction augments the efficacy of enzyme therapy in a mouse model of Fabry diseaseJohn Marshall, Karen M Ashe, Dinesh Bangari, et al.
Molecular Medicine (Cambridge, Mass.)|May 5, 2015
Efficacy of Enzyme and Substrate Reduction Therapy with a Novel Antagonist of Glucosylceramide Synthase for Fabry DiseaseKaren M Ashe, Eva Budman, Dinesh S Bangari, et al.
Human Gene Therapy|May 27, 2008
Ability of adeno-associated virus serotype 8-mediated hepatic expression of acid alpha-glucosidase to correct the biochemical and motor function deficits of presymptomatic and symptomatic Pompe miceRobin J Ziegler, Scott D Bercury, Jonathan Fidler, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 30, 2011
Systemic administration of AAV8-α-galactosidase A induces humoral tolerance in nonhuman primates despite low hepatic expressionJennifer B Nietupski, Gregory D Hurlbut, Robin J Ziegler, et al.
Pageof 5