Search research articles
Contact Us
Filters
Showing results (51-60 of 62) with videos related to
Page
of 7
Sort By:
Journal of Neuromuscular Diseases
|
July 9, 2026
2025 update of the National French consensus on gene lists for the diagnosis of muscle diseases using high-throughput sequencing
Emmanuelle Pion, Mireille Cossée, Valérie Biancalana, et al.
European Journal of Human Genetics : EJHG
|
December 16, 2018
A National French consensus on gene lists for the diagnosis of myopathies using next-generation sequencing
Martin Krahn, Valérie Biancalana, Mathieu Cerino, et al.
Journal of Inherited Metabolic Disease
|
February 17, 2026
Expert-Designed Fact Sheets and AI-Based Analysis of Patient Symptoms to Combat Diagnostic Delays in Inherited Metabolic Diseases
Aline Cano, Xiaoyi Chen, Azza Khemiri, et al.
Orphanet Journal of Rare Diseases
|
October 28, 2025
French national diagnosis and care protocol (Protocole National De Diagnostic et de Soins; PNDS): Gaucher disease
Fabrice Camou, Christine Serratrice, Magali Pettazzoni, et al.
Orphanet Journal of Rare Diseases
|
August 2, 2018
Deep characterization of the anti-drug antibodies developed in Fabry disease patients, a prospective analysis from the French multicenter cohort FFABRY
Wladimir Mauhin, Olivier Lidove, Damien Amelin, et al.
Neurology
|
July 25, 2019
Brain MRI features and scoring of leukodystrophy in adult-onset Krabbe disease
Louis Cousyn, Bruno Law-Ye, Nadya Pyatigorskaya, et al.
Annals of Neurology
|
October 5, 2012
Adult polyglucosan body disease: Natural History and Key Magnetic Resonance Imaging Findings
Fanny Mochel, Raphael Schiffmann, Marjan E Steenweg, et al.
Journal of Clinical Medicine
|
July 26, 2020
A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease
Christine Serratrice, Jérôme Stirnemann, Amina Berrahal, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 9, 2010
Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromes
N Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris, et al.
European Journal of Neurology
|
May 26, 2023
Long-term follow-up of 64 children with classical infantile-onset Pompe disease since 2004: A French real-life observational study
Marine Tardieu, Céline Cudejko, Aline Cano, et al.
Page
of 7
Search research articles
Search
Showing results (51-60 of 62) with videos related to
Sort By:
Page
of 7
Journal of Neuromuscular Diseases
|
July 9, 2026
2025 update of the National French consensus on gene lists for the diagnosis of muscle diseases using high-throughput sequencing
Emmanuelle Pion, Mireille Cossée, Valérie Biancalana, et al.
European Journal of Human Genetics : EJHG
|
December 16, 2018
A National French consensus on gene lists for the diagnosis of myopathies using next-generation sequencing
Martin Krahn, Valérie Biancalana, Mathieu Cerino, et al.
Journal of Inherited Metabolic Disease
|
February 17, 2026
Expert-Designed Fact Sheets and AI-Based Analysis of Patient Symptoms to Combat Diagnostic Delays in Inherited Metabolic Diseases
Aline Cano, Xiaoyi Chen, Azza Khemiri, et al.
Orphanet Journal of Rare Diseases
|
October 28, 2025
French national diagnosis and care protocol (Protocole National De Diagnostic et de Soins; PNDS): Gaucher disease
Fabrice Camou, Christine Serratrice, Magali Pettazzoni, et al.
Orphanet Journal of Rare Diseases
|
August 2, 2018
Deep characterization of the anti-drug antibodies developed in Fabry disease patients, a prospective analysis from the French multicenter cohort FFABRY
Wladimir Mauhin, Olivier Lidove, Damien Amelin, et al.
Neurology
|
July 25, 2019
Brain MRI features and scoring of leukodystrophy in adult-onset Krabbe disease
Louis Cousyn, Bruno Law-Ye, Nadya Pyatigorskaya, et al.
Annals of Neurology
|
October 5, 2012
Adult polyglucosan body disease: Natural History and Key Magnetic Resonance Imaging Findings
Fanny Mochel, Raphael Schiffmann, Marjan E Steenweg, et al.
Journal of Clinical Medicine
|
July 26, 2020
A Cross-Sectional Retrospective Study of Non-Splenectomized and Never-Treated Patients with Type 1 Gaucher Disease
Christine Serratrice, Jérôme Stirnemann, Amina Berrahal, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
December 9, 2010
Safe, efficient, and reproducible gene therapy of the brain in the dog models of Sanfilippo and Hurler syndromes
N Matthew Ellinwood, Jérôme Ausseil, Nathalie Desmaris, et al.
European Journal of Neurology
|
May 26, 2023
Long-term follow-up of 64 children with classical infantile-onset Pompe disease since 2004: A French real-life observational study
Marine Tardieu, Céline Cudejko, Aline Cano, et al.
Page
of 7