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Annals of Neurology
|
February 27, 2013
LTBP4 genotype predicts age of ambulatory loss in Duchenne muscular dystrophy
Kevin M Flanigan, Ermelinda Ceco, Kay-Marie Lamar, et al.
Journal of Neuromuscular Diseases
|
January 22, 2024
Real-World Outcomes in Patients with Spinal Muscular Atrophy Treated with Onasemnogene Abeparvovec Monotherapy: Findings from the RESTORE Registry
Laurent Servais, John W Day, Darryl C De Vivo, et al.
Plos One
|
September 10, 2014
Magnetic resonance imaging and spectroscopy assessment of lower extremity skeletal muscles in boys with Duchenne muscular dystrophy: a multicenter cross sectional study
Sean C Forbes, Rebecca J Willcocks, William T Triplett, et al.
Annals of Neurology
|
February 20, 2016
Multicenter prospective longitudinal study of magnetic resonance biomarkers in a large duchenne muscular dystrophy cohort
Rebecca J Willcocks, William D Rooney, William T Triplett, et al.
Lancet (London, England)
|
March 13, 2022
Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial
Craig M McDonald, Eduardo Marbán, Suzanne Hendrix, et al.
BMJ Neurology Open
|
April 1, 2026
Peripheral frataxin levels govern long-term clinical progression in Friedreich ataxia
Christian Rummey, Ian A Blair, Clementina Mesaros, et al.
Muscle & Nerve
|
February 2, 2019
Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy
Anne M Connolly, Craig M Zaidman, Paul T Golumbek, et al.
Annals of Neurology
|
January 23, 2015
Clinical phenotypes as predictors of the outcome of skipping around DMD exon 45
Andrew R Findlay, Nicolas Wein, Yuuki Kaminoh, et al.
Brain : a Journal of Neurology
|
June 25, 2024
TRPV4 neuromuscular disease registry highlights bulbar, skeletal and proximal limb manifestations
Gage P Kosmanopoulos, Jack K Donohue, Maya Hoke, et al.
The New England Journal of Medicine
|
November 2, 2017
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Richard S Finkel, Eugenio Mercuri, Basil T Darras, et al.
Page
of 29
Search research articles
Search
Showing results (211-220 of 289) with videos related to
Sort By:
Page
of 29
Annals of Neurology
|
February 27, 2013
LTBP4 genotype predicts age of ambulatory loss in Duchenne muscular dystrophy
Kevin M Flanigan, Ermelinda Ceco, Kay-Marie Lamar, et al.
Journal of Neuromuscular Diseases
|
January 22, 2024
Real-World Outcomes in Patients with Spinal Muscular Atrophy Treated with Onasemnogene Abeparvovec Monotherapy: Findings from the RESTORE Registry
Laurent Servais, John W Day, Darryl C De Vivo, et al.
Plos One
|
September 10, 2014
Magnetic resonance imaging and spectroscopy assessment of lower extremity skeletal muscles in boys with Duchenne muscular dystrophy: a multicenter cross sectional study
Sean C Forbes, Rebecca J Willcocks, William T Triplett, et al.
Annals of Neurology
|
February 20, 2016
Multicenter prospective longitudinal study of magnetic resonance biomarkers in a large duchenne muscular dystrophy cohort
Rebecca J Willcocks, William D Rooney, William T Triplett, et al.
Lancet (London, England)
|
March 13, 2022
Repeated intravenous cardiosphere-derived cell therapy in late-stage Duchenne muscular dystrophy (HOPE-2): a multicentre, randomised, double-blind, placebo-controlled, phase 2 trial
Craig M McDonald, Eduardo Marbán, Suzanne Hendrix, et al.
BMJ Neurology Open
|
April 1, 2026
Peripheral frataxin levels govern long-term clinical progression in Friedreich ataxia
Christian Rummey, Ian A Blair, Clementina Mesaros, et al.
Muscle & Nerve
|
February 2, 2019
Twice-weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy
Anne M Connolly, Craig M Zaidman, Paul T Golumbek, et al.
Annals of Neurology
|
January 23, 2015
Clinical phenotypes as predictors of the outcome of skipping around DMD exon 45
Andrew R Findlay, Nicolas Wein, Yuuki Kaminoh, et al.
Brain : a Journal of Neurology
|
June 25, 2024
TRPV4 neuromuscular disease registry highlights bulbar, skeletal and proximal limb manifestations
Gage P Kosmanopoulos, Jack K Donohue, Maya Hoke, et al.
The New England Journal of Medicine
|
November 2, 2017
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Richard S Finkel, Eugenio Mercuri, Basil T Darras, et al.
Page
of 29