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Microbiology Resource Announcements
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November 6, 2020
Genome Sequences of Microbacteriophages Zada and Ioannes
Razan El Yaman, Jayla S Anderson, Tania M Anderson, et al.
Muscle & Nerve
|
July 6, 2023
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5-year update of the NURTURE study
Thomas O Crawford, Kathryn J Swoboda, Darryl C De Vivo, et al.
Plos One
|
June 27, 2018
Ambulatory function in spinal muscular atrophy: Age-related patterns of progression
Jacqueline Montes, Michael P McDermott, Elizabeth Mirek, et al.
Lancet (London, England)
|
July 22, 2017
Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig M McDonald, Craig Campbell, Ricardo Erazo Torricelli, et al.
Annals of Neurology
|
October 7, 2022
Disease Progression in Charcot-Marie-Tooth Disease Related to MPZ Mutations: A Longitudinal Study
Vera Fridman, Stefan Sillau, Jacob Bockhorst, et al.
Neuromuscular Disorders : NMD
|
July 16, 2010
Clinical and genetic characterization of manifesting carriers of DMD mutations
Payam Soltanzadeh, Michael J Friez, Diane Dunn, et al.
Plos Medicine
|
September 21, 2020
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Edward C Smith, Laurie S Conklin, Eric P Hoffman, et al.
The Lancet. Neurology
|
August 16, 2025
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial
Thomas O Crawford, Laurent Servais, Eugenio Mercuri, et al.
Human Mutation
|
November 26, 2009
Mutational spectrum of DMD mutations in dystrophinopathy patients: application of modern diagnostic techniques to a large cohort
Kevin M Flanigan, Diane M Dunn, Andrew von Niederhausern, et al.
Neuromuscular Disorders : NMD
|
November 10, 2019
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Darryl C De Vivo, Enrico Bertini, Kathryn J Swoboda, et al.
Page
of 29
Search research articles
Search
Showing results (251-260 of 289) with videos related to
Sort By:
Page
of 29
Microbiology Resource Announcements
|
November 6, 2020
Genome Sequences of Microbacteriophages Zada and Ioannes
Razan El Yaman, Jayla S Anderson, Tania M Anderson, et al.
Muscle & Nerve
|
July 6, 2023
Continued benefit of nusinersen initiated in the presymptomatic stage of spinal muscular atrophy: 5-year update of the NURTURE study
Thomas O Crawford, Kathryn J Swoboda, Darryl C De Vivo, et al.
Plos One
|
June 27, 2018
Ambulatory function in spinal muscular atrophy: Age-related patterns of progression
Jacqueline Montes, Michael P McDermott, Elizabeth Mirek, et al.
Lancet (London, England)
|
July 22, 2017
Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Craig M McDonald, Craig Campbell, Ricardo Erazo Torricelli, et al.
Annals of Neurology
|
October 7, 2022
Disease Progression in Charcot-Marie-Tooth Disease Related to MPZ Mutations: A Longitudinal Study
Vera Fridman, Stefan Sillau, Jacob Bockhorst, et al.
Neuromuscular Disorders : NMD
|
July 16, 2010
Clinical and genetic characterization of manifesting carriers of DMD mutations
Payam Soltanzadeh, Michael J Friez, Diane Dunn, et al.
Plos Medicine
|
September 21, 2020
Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study
Edward C Smith, Laurie S Conklin, Eric P Hoffman, et al.
The Lancet. Neurology
|
August 16, 2025
Safety and efficacy of apitegromab in nonambulatory type 2 or type 3 spinal muscular atrophy (SAPPHIRE): a phase 3, double-blind, randomised, placebo-controlled trial
Thomas O Crawford, Laurent Servais, Eugenio Mercuri, et al.
Human Mutation
|
November 26, 2009
Mutational spectrum of DMD mutations in dystrophinopathy patients: application of modern diagnostic techniques to a large cohort
Kevin M Flanigan, Diane M Dunn, Andrew von Niederhausern, et al.
Neuromuscular Disorders : NMD
|
November 10, 2019
Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study
Darryl C De Vivo, Enrico Bertini, Kathryn J Swoboda, et al.
Page
of 29