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Pediatric Pulmonology|March 11, 2015
Characterization of pulmonary function in Duchenne Muscular DystrophyO H Mayer, R S Finkel, C Rummey, et al.Annals of Neurology|March 9, 2023
Trials for Slowly Progressive Neurogenetic Diseases Need Surrogate EndpointsMary M Reilly, David N Herrmann, Davide Pareyson, et al.Molecular Therapy. Methods & Clinical Development|March 26, 2021
Adeno-associated virus serotype 9 antibodies in patients screened for treatment with onasemnogene abeparvovecJohn W Day, Richard S Finkel, Eugenio Mercuri, et al.CNS Drugs|August 18, 2019
An Integrated Safety Analysis of Infants and Children with Symptomatic Spinal Muscular Atrophy (SMA) Treated with Nusinersen in Seven Clinical TrialsBasil T Darras, Michelle A Farrar, Eugenio Mercuri, et al.American Journal of Medical Genetics. Part C, Seminars in Medical Genetics|January 3, 2023
Data sharing to advance gene-targeted therapies in rare diseasesJulie Lekstrom-Himes, Erika F Augustine, Amy Brower, et al.Muscle & Nerve|March 20, 2026
Motor Function and Growth Outcomes With Early Corticosteroid Initiation in Duchenne Muscular Dystrophy: An Adjusted Cross-Trial ComparisonEmma Ciafaloni, Abigail Zion, Joanne Donovan, et al.Neuromuscular Disorders : NMD|September 18, 2012
MRI/MRS evaluation of a female carrier of Duchenne muscular dystrophySean C Forbes, Donovan J Lott, Richard S Finkel, et al.Journal of the European Academy of Dermatology and Venereology : JEADV|June 26, 2019
Incidence and prevalence of psoriasis in Israel between 2011 and 2017Y Schonmann, D M Ashcroft, I Y K Iskandar, et al.Neurology|February 17, 2006
SMN mRNA and protein levels in peripheral blood: biomarkers for SMA clinical trialsC J Sumner, S J Kolb, G G Harmison, et al.Pediatric Physical Therapy : the Official Publication of the Section on Pediatrics of the American Physical Therapy Association|August 16, 2008
The test of infant motor performance: reliability in spinal muscular atrophy type IRichard S Finkel, Linda S Hynan, Allan M Glanzman, et al.Pageof 38