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Archivio Italiano Di Urologia, Andrologia : Organo Ufficiale [Di] Societa Italiana Di Ecografia Urologica E Nefrologica|March 16, 2023
Determinants of renal papillary appearance in kidney stone formers: An in-depth examinationMatteo Bargagli, Francesco Pinto, Rossella De Leonardis, et al.
Journal of Clinical Immunology|April 21, 2020
Urogenital Abnormalities in Adenosine Deaminase DeficiencyRoberta Pajno, Lucia Pacillo, Salvatore Recupero, et al.
Brain : a Journal of Neurology|April 26, 2025
Effects of atidarsagene autotemcel gene therapy on peripheral nerves in late-infantile metachromatic leukodystrophyAlberto A Zambon, Paola M V Rancoita, Angelo Quattrini, et al.
Journal of Inherited Metabolic Disease|April 15, 2021
Metachromatic leukodystrophy: A single-center longitudinal study of 45 patientsFrancesca Fumagalli, Alberto A Zambon, Paola M V Rancoita, et al.
Biomedicines|July 29, 2023
Outcome of BCG Vaccination in ADA-SCID Patients: A 12-Patient SeriesDaniele Canarutto, Chiara Oltolini, Federica Barzaghi, et al.
Frontiers in Immunology|July 12, 2023
Hemophagocytic inflammatory syndrome in ADA-SCID: report of two cases and literature reviewElena Sophia Fratini, Maddalena Migliavacca, Federica Barzaghi, et al.
Bone Marrow Transplantation|June 1, 2019
Bone marrow harvesting from paediatric patients undergoing haematopoietic stem cell gene therapyFrancesca Tucci, Marta Frittoli, Federica Barzaghi, et al.
Science Translational Medicine|May 1, 2024
Early skeletal outcomes after hematopoietic stem and progenitor cell gene therapy for Hurler syndromeGiulia Consiglieri, Francesca Tucci, Maurizio De Pellegrin, et al.
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