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The New England Journal of Medicine|April 23, 2025
Long-Term Effects of Atidarsagene Autotemcel for Metachromatic LeukodystrophyFrancesca Fumagalli, Valeria Calbi, Vera Gallo, et al.Nature Medicine|February 15, 2024
Long-term and real-world safety and efficacy of retroviral gene therapy for adenosine deaminase deficiencyMaddalena Migliavacca, Federica Barzaghi, Claudia Fossati, et al.Pageof 2