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Molecular Therapy : the Journal of the American Society of Gene Therapy|December 16, 2010
Adeno-associated virus vectors serotype 2 induce prolonged proliferation of capsid-specific CD8+ T cells in miceHua Li, Steven Tuyishime, Te-Lang Wu, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|June 15, 2007
Persistent expression of hF.IX After tolerance induction by in utero or neonatal administration of AAV-1-F.IX in hemophilia B miceDenise E Sabatino, Tippi C Mackenzie, William Peranteau, et al.
Human Gene Therapy|August 21, 2004
Therapeutic levels of factor IX expression using a muscle-specific promoter and adeno-associated virus serotype 1 vectorYi-Lin Liu, Federico Mingozzi, Sol M Rodriguéz-Colôn, et al.
Blood|February 18, 2011
Catalytic domain modification and viral gene delivery of activated factor VII confers hemostasis at reduced expression levels and vector doses in vivoParis Margaritis, Elise Roy, Armida Faella, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|March 19, 2009
Host and vector-dependent effects on the risk of germline transmission of AAV vectorsPatricia Favaro, Harre D Downey, J Shangzhen Zhou, et al.
Molecular Therapy. Methods & Clinical Development|March 19, 2025
Validation of a quantitative cell-based relative potency assay for LUXTURNAKatherine A High, Dave Le Blond, Karen Doucette, et al.
Nature|June 28, 2011
In vivo genome editing restores haemostasis in a mouse model of haemophiliaHojun Li, Virginia Haurigot, Yannick Doyon, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|December 22, 2011
Self-complementary AAVs induce more potent transgene product-specific immune responses compared to a single-stranded genomeTeLang Wu, Katrin Töpfer, Shih-Wen Lin, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|October 1, 2013
CD8+ T cell recognition of epitopes within the capsid of adeno-associated virus 8-based gene transfer vectors depends on vectors' genomeTe-Lang Wu, Hua Li, Susan M Faust, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy|April 16, 2009
A preclinical animal model to assess the effect of pre-existing immunity on AAV-mediated gene transferHua Li, Shih-Wen Lin, Wynetta Giles-Davis, et al.
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