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American Journal of Medical Genetics. Part A
|
June 19, 2025
The Expanding Clinical and Genetic Spectrum of Muscle Glycogen Storage Disease 0, (GSD0B)
Sarah Donoghue, Smitha Kumble, Pontus Wasling, et al.
Human Mutation
|
September 9, 2020
Rapid exome sequencing and adjunct RNA studies confirm the pathogenicity of a novel homozygous ASNS splicing variant in a critically ill neonate
Lauren S Akesson, Adam Bournazos, Andrew Fennell, et al.
Human Molecular Genetics
|
March 15, 2023
Connective tissue presentation in two families expands the phenotypic spectrum of PYROXD1 disorders
Frances J Evesson, Gregory Dziaduch, Samantha J Bryen, et al.
American Journal of Human Genetics
|
August 27, 2019
Pathogenic Abnormal Splicing Due to Intronic Deletions that Induce Biophysical Space Constraint for Spliceosome Assembly
Samantha J Bryen, Himanshu Joshi, Frances J Evesson, et al.
Human Molecular Genetics
|
August 27, 2015
Muscle weakness in TPM3-myopathy is due to reduced Ca2+-sensitivity and impaired acto-myosin cross-bridge cycling in slow fibres
Michaela Yuen, Sandra T Cooper, Steve B Marston, et al.
Neurology
|
October 28, 2025
Expert Consensus on Genetic Diagnostic Approaches for Patients With Limb-Girdle Muscular Dystrophy
Volker Straub, Amanda R Clause, Sandra Donkervoort, et al.
Human Mutation
|
June 29, 2010
Recessive mutations in RYR1 are a common cause of congenital fiber type disproportion
Nigel F Clarke, Leigh B Waddell, Sandra T Cooper, et al.
Journal of Neuropathology and Experimental Neurology
|
March 18, 2011
Dysferlin, annexin A1, and mitsugumin 53 are upregulated in muscular dystrophy and localize to longitudinal tubules of the T-system with stretch
Leigh B Waddell, Frances A Lemckert, Xi F Zheng, et al.
Neurology
|
September 4, 2016
Variants in SLC18A3, vesicular acetylcholine transporter, cause congenital myasthenic syndrome
Gina L O'Grady, Corien Verschuuren, Michaela Yuen, et al.
JAMA Neurology
|
October 6, 2015
Use of Whole-Exome Sequencing for Diagnosis of Limb-Girdle Muscular Dystrophy: Outcomes and Lessons Learned
Roula Ghaoui, Sandra T Cooper, Monkol Lek, et al.
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Search research articles
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Showing results (61-70 of 97) with videos related to
Sort By:
Page
of 10
American Journal of Medical Genetics. Part A
|
June 19, 2025
The Expanding Clinical and Genetic Spectrum of Muscle Glycogen Storage Disease 0, (GSD0B)
Sarah Donoghue, Smitha Kumble, Pontus Wasling, et al.
Human Mutation
|
September 9, 2020
Rapid exome sequencing and adjunct RNA studies confirm the pathogenicity of a novel homozygous ASNS splicing variant in a critically ill neonate
Lauren S Akesson, Adam Bournazos, Andrew Fennell, et al.
Human Molecular Genetics
|
March 15, 2023
Connective tissue presentation in two families expands the phenotypic spectrum of PYROXD1 disorders
Frances J Evesson, Gregory Dziaduch, Samantha J Bryen, et al.
American Journal of Human Genetics
|
August 27, 2019
Pathogenic Abnormal Splicing Due to Intronic Deletions that Induce Biophysical Space Constraint for Spliceosome Assembly
Samantha J Bryen, Himanshu Joshi, Frances J Evesson, et al.
Human Molecular Genetics
|
August 27, 2015
Muscle weakness in TPM3-myopathy is due to reduced Ca2+-sensitivity and impaired acto-myosin cross-bridge cycling in slow fibres
Michaela Yuen, Sandra T Cooper, Steve B Marston, et al.
Neurology
|
October 28, 2025
Expert Consensus on Genetic Diagnostic Approaches for Patients With Limb-Girdle Muscular Dystrophy
Volker Straub, Amanda R Clause, Sandra Donkervoort, et al.
Human Mutation
|
June 29, 2010
Recessive mutations in RYR1 are a common cause of congenital fiber type disproportion
Nigel F Clarke, Leigh B Waddell, Sandra T Cooper, et al.
Journal of Neuropathology and Experimental Neurology
|
March 18, 2011
Dysferlin, annexin A1, and mitsugumin 53 are upregulated in muscular dystrophy and localize to longitudinal tubules of the T-system with stretch
Leigh B Waddell, Frances A Lemckert, Xi F Zheng, et al.
Neurology
|
September 4, 2016
Variants in SLC18A3, vesicular acetylcholine transporter, cause congenital myasthenic syndrome
Gina L O'Grady, Corien Verschuuren, Michaela Yuen, et al.
JAMA Neurology
|
October 6, 2015
Use of Whole-Exome Sequencing for Diagnosis of Limb-Girdle Muscular Dystrophy: Outcomes and Lessons Learned
Roula Ghaoui, Sandra T Cooper, Monkol Lek, et al.
Page
of 10