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Neuromuscular Disorders : NMD
|
June 24, 2025
Multi-omics approach identifies a novel recessive pathogenic variant in the TNNT3 gene in two siblings with congenital myopathy
Juliane S Müller, Shira Rabinowicz, Irina Zaharieva, et al.
Neuromuscular Disorders : NMD
|
July 9, 2013
DOK7 congenital myasthenic syndrome in childhood: early diagnostic clues in 23 children
Andrea Klein, Matthew C Pitt, John C McHugh, et al.
Neurology
|
October 24, 2014
Clinical spectrum of 4H leukodystrophy caused by POLR3A and POLR3B mutations
Nicole I Wolf, Adeline Vanderver, Rosalina M L van Spaendonk, et al.
The Lancet Regional Health. Europe
|
January 3, 2024
Efficacy and safety of onasemnogene abeparvovec in children with spinal muscular atrophy type 1: real-world evidence from 6 infusion centres in the United Kingdom
Vasantha Gowda, Mark Atherton, Archana Murugan, et al.
Acta Neuropathologica
|
January 15, 2021
Making sense of missense variants in TTN-related congenital myopathies
Martin Rees, Roksana Nikoopour, Atsushi Fukuzawa, et al.
The Journal of Clinical Endocrinology and Metabolism
|
October 2, 2020
Endocrine and Growth Abnormalities in 4H Leukodystrophy Caused by Variants in POLR3A, POLR3B, and POLR1C
Félixe Pelletier, Stefanie Perrier, Ferdy K Cayami, et al.
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Search research articles
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Showing results (11-20 of 16) with videos related to
Sort By:
Page
of 2
You have reached the last page of results.
This site can display upto 16 results.
Neuromuscular Disorders : NMD
|
June 24, 2025
Multi-omics approach identifies a novel recessive pathogenic variant in the TNNT3 gene in two siblings with congenital myopathy
Juliane S Müller, Shira Rabinowicz, Irina Zaharieva, et al.
Neuromuscular Disorders : NMD
|
July 9, 2013
DOK7 congenital myasthenic syndrome in childhood: early diagnostic clues in 23 children
Andrea Klein, Matthew C Pitt, John C McHugh, et al.
Neurology
|
October 24, 2014
Clinical spectrum of 4H leukodystrophy caused by POLR3A and POLR3B mutations
Nicole I Wolf, Adeline Vanderver, Rosalina M L van Spaendonk, et al.
The Lancet Regional Health. Europe
|
January 3, 2024
Efficacy and safety of onasemnogene abeparvovec in children with spinal muscular atrophy type 1: real-world evidence from 6 infusion centres in the United Kingdom
Vasantha Gowda, Mark Atherton, Archana Murugan, et al.
Acta Neuropathologica
|
January 15, 2021
Making sense of missense variants in TTN-related congenital myopathies
Martin Rees, Roksana Nikoopour, Atsushi Fukuzawa, et al.
The Journal of Clinical Endocrinology and Metabolism
|
October 2, 2020
Endocrine and Growth Abnormalities in 4H Leukodystrophy Caused by Variants in POLR3A, POLR3B, and POLR1C
Félixe Pelletier, Stefanie Perrier, Ferdy K Cayami, et al.
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