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Nature
|
May 30, 2014
CTP synthase 1 deficiency in humans reveals its central role in lymphocyte proliferation
Emmanuel Martin, Noé Palmic, Sylvia Sanquer, et al.
Blood
|
March 10, 2021
The equilibrative nucleoside transporter ENT1 is critical for nucleotide homeostasis and optimal erythropoiesis
Mahmoud Mikdar, Pedro González-Menéndez, Xiaoli Cai, et al.
JCI Insight
|
March 13, 2020
Impaired lymphocyte function and differentiation in CTPS1-deficient patients result from a hypomorphic homozygous mutation
Emmanuel Martin, Norbert Minet, Anne-Claire Boschat, et al.
European Journal of Medical Genetics
|
August 12, 2020
PRPS1 loss-of-function variants, from isolated hearing loss to severe congenital encephalopathy: New cases and literature review
Oriane Mercati, Marie-Thérèse Abi Warde, Geneviève Lina-Granade, et al.
Movement Disorders Clinical Practice
|
May 19, 2023
Intraputaminal Gene Delivery in Two Patients with Aromatic L-Amino Acid Decarboxylase Deficiency
Marie-Céline François-Heude, Gaetan Poulen, Emmanuel Flamand Roze, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
July 2, 2026
Gene Therapy for Amino Acid Decarboxylase Deficiency: Clinical and Imaging Outcomes in a French Cohort
Clément Dunoyer, Gaëtan Poulen, Marie-Céline François-Heude, et al.
Nature Communications
|
September 5, 2019
Defects in t<sup>6</sup>A tRNA modification due to GON7 and YRDC mutations lead to Galloway-Mowat syndrome
Christelle Arrondel, Sophia Missoury, Rozemarijn Snoek, et al.
Journal of Clinical Immunology
|
May 12, 2023
JAK Inhibition in Aicardi-Goutières Syndrome: a Monocentric Multidisciplinary Real-World Approach Study
Marie-Louise Frémond, Marie Hully, Benjamin Fournier, et al.
The Lancet. Neurology
|
February 22, 2025
Autoinflammatory encephalopathy due to PTPN1 haploinsufficiency: a case series
Gaofeng Zhu, Blaise Didry-Barca, Luis Seabra, et al.
Nature Genetics
|
August 15, 2017
Mutations in KEOPS-complex genes cause nephrotic syndrome with primary microcephaly
Daniela A Braun, Jia Rao, Geraldine Mollet, et al.
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Search research articles
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Showing results (71-80 of 80) with videos related to
Sort By:
Page
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You have reached the last page of results.
This site can display upto 80 results.
Nature
|
May 30, 2014
CTP synthase 1 deficiency in humans reveals its central role in lymphocyte proliferation
Emmanuel Martin, Noé Palmic, Sylvia Sanquer, et al.
Blood
|
March 10, 2021
The equilibrative nucleoside transporter ENT1 is critical for nucleotide homeostasis and optimal erythropoiesis
Mahmoud Mikdar, Pedro González-Menéndez, Xiaoli Cai, et al.
JCI Insight
|
March 13, 2020
Impaired lymphocyte function and differentiation in CTPS1-deficient patients result from a hypomorphic homozygous mutation
Emmanuel Martin, Norbert Minet, Anne-Claire Boschat, et al.
European Journal of Medical Genetics
|
August 12, 2020
PRPS1 loss-of-function variants, from isolated hearing loss to severe congenital encephalopathy: New cases and literature review
Oriane Mercati, Marie-Thérèse Abi Warde, Geneviève Lina-Granade, et al.
Movement Disorders Clinical Practice
|
May 19, 2023
Intraputaminal Gene Delivery in Two Patients with Aromatic L-Amino Acid Decarboxylase Deficiency
Marie-Céline François-Heude, Gaetan Poulen, Emmanuel Flamand Roze, et al.
Movement Disorders : Official Journal of the Movement Disorder Society
|
July 2, 2026
Gene Therapy for Amino Acid Decarboxylase Deficiency: Clinical and Imaging Outcomes in a French Cohort
Clément Dunoyer, Gaëtan Poulen, Marie-Céline François-Heude, et al.
Nature Communications
|
September 5, 2019
Defects in t<sup>6</sup>A tRNA modification due to GON7 and YRDC mutations lead to Galloway-Mowat syndrome
Christelle Arrondel, Sophia Missoury, Rozemarijn Snoek, et al.
Journal of Clinical Immunology
|
May 12, 2023
JAK Inhibition in Aicardi-Goutières Syndrome: a Monocentric Multidisciplinary Real-World Approach Study
Marie-Louise Frémond, Marie Hully, Benjamin Fournier, et al.
The Lancet. Neurology
|
February 22, 2025
Autoinflammatory encephalopathy due to PTPN1 haploinsufficiency: a case series
Gaofeng Zhu, Blaise Didry-Barca, Luis Seabra, et al.
Nature Genetics
|
August 15, 2017
Mutations in KEOPS-complex genes cause nephrotic syndrome with primary microcephaly
Daniela A Braun, Jia Rao, Geraldine Mollet, et al.
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