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Journal of Child Neurology
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May 14, 2025
Exploration Into Lived Experiences of Multiple Sulfatase Deficiency-Affected Individuals and Their Families
Francesco Gavazzi, Emily Yu, Zarrin Tashnim, et al.
Journal of Child Neurology
|
September 28, 2019
Developmental Outcomes of Aicardi Goutières Syndrome
Laura Adang, Francesco Gavazzi, Micaela De Simone, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 22, 2026
Therapeutic suppression of Tubb4a rescues H-ABC leukodystrophy
Sunetra Sase, Julia L Hacker, Prabhat R Napit, et al.
Journal of Child Neurology
|
March 27, 2024
Characterization of Fine Motor and Visual Motor Skills in Aicardi-Goutières Syndrome
Stacy V Cusack, Francesco Gavazzi, Isabella Peixoto de Barcelos, et al.
Molecular Genetics and Metabolism
|
November 5, 2022
SARS-CoV-2 mRNA-based vaccines in the Aicardi Goutières Syndrome
Asako Takanohashi, Mohamad-Gabriel Alameh, Sarah Woidill, et al.
Molecular Genetics and Metabolism
|
March 5, 2026
Design of a Pediatric Low Motor Function Item Battery in leukodystrophies
Francesco Gavazzi, Sarah Woidill, Anjana Sevagamoorthy, et al.
Molecular Genetics and Metabolism
|
October 16, 2025
Functional ability profiles in beta-propeller protein-associated neurodegeneration (BPAN)
Francesco Gavazzi, Samuel R Pierce, Vanessa Smith, et al.
Human Mutation
|
March 4, 2020
Type II Alexander disease caused by splicing errors and aberrant overexpression of an uncharacterized GFAP isoform
Guy Helman, Asako Takanohashi, Tracy L Hagemann, et al.
Human Mutation
|
August 3, 2022
Type II Alexander disease caused by splicing errors and aberrant overexpression of an uncharacterized GFAP isoform
Guy Helman, Asako Takanohashi, Tracy L Hagemann, et al.
Pediatric Neurology
|
October 23, 2025
Critical Functional Domains in Pediatric Onset TUBB4A-Related Leukodystrophy: A Clinical and Caregiver's Perspective
Francesco Gavazzi, Virali Patel, Jacqueline A Erler, et al.
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of 4
Search research articles
Search
Showing results (11-20 of 32) with videos related to
Sort By:
Page
of 4
Journal of Child Neurology
|
May 14, 2025
Exploration Into Lived Experiences of Multiple Sulfatase Deficiency-Affected Individuals and Their Families
Francesco Gavazzi, Emily Yu, Zarrin Tashnim, et al.
Journal of Child Neurology
|
September 28, 2019
Developmental Outcomes of Aicardi Goutières Syndrome
Laura Adang, Francesco Gavazzi, Micaela De Simone, et al.
Molecular Therapy : the Journal of the American Society of Gene Therapy
|
January 22, 2026
Therapeutic suppression of Tubb4a rescues H-ABC leukodystrophy
Sunetra Sase, Julia L Hacker, Prabhat R Napit, et al.
Journal of Child Neurology
|
March 27, 2024
Characterization of Fine Motor and Visual Motor Skills in Aicardi-Goutières Syndrome
Stacy V Cusack, Francesco Gavazzi, Isabella Peixoto de Barcelos, et al.
Molecular Genetics and Metabolism
|
November 5, 2022
SARS-CoV-2 mRNA-based vaccines in the Aicardi Goutières Syndrome
Asako Takanohashi, Mohamad-Gabriel Alameh, Sarah Woidill, et al.
Molecular Genetics and Metabolism
|
March 5, 2026
Design of a Pediatric Low Motor Function Item Battery in leukodystrophies
Francesco Gavazzi, Sarah Woidill, Anjana Sevagamoorthy, et al.
Molecular Genetics and Metabolism
|
October 16, 2025
Functional ability profiles in beta-propeller protein-associated neurodegeneration (BPAN)
Francesco Gavazzi, Samuel R Pierce, Vanessa Smith, et al.
Human Mutation
|
March 4, 2020
Type II Alexander disease caused by splicing errors and aberrant overexpression of an uncharacterized GFAP isoform
Guy Helman, Asako Takanohashi, Tracy L Hagemann, et al.
Human Mutation
|
August 3, 2022
Type II Alexander disease caused by splicing errors and aberrant overexpression of an uncharacterized GFAP isoform
Guy Helman, Asako Takanohashi, Tracy L Hagemann, et al.
Pediatric Neurology
|
October 23, 2025
Critical Functional Domains in Pediatric Onset TUBB4A-Related Leukodystrophy: A Clinical and Caregiver's Perspective
Francesco Gavazzi, Virali Patel, Jacqueline A Erler, et al.
Page
of 4