Showing results (11-20 of 28) with videos related to
Sort By:
Pageof 3
International Journal of Molecular Sciences|March 29, 2023
Prevalence of Neutralizing Antibodies against Adeno-Associated Virus Serotypes 1, 2, and 9 in Non-Injected Latin American Patients with Heart Failure-ANVIAS StudyJulieth A Sierra-Delgado, Shibi Likhite, Paula K Bautista, et al.Journal of Biomedical Science|January 4, 2026
AAV9 gene therapy optimization for SMARD1/CMT2S: safety and long-term efficacy comparison of two vectors in a SMARD1 preclinical modelElisa Pagliari, Alessia Anastasia, Floriana Bellandi, et al.Nature Medicine|March 2, 2016
Major histocompatibility complex class I molecules protect motor neurons from astrocyte-induced toxicity in amyotrophic lateral sclerosisSungWon Song, Carlos J Miranda, Lyndsey Braun, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|November 1, 2014
Improving single injection CSF delivery of AAV9-mediated gene therapy for SMA: a dose-response study in mice and nonhuman primatesKathrin Meyer, Laura Ferraiuolo, Leah Schmelzer, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|October 4, 2020
AAV9 Gene Therapy Increases Lifespan and Treats Pathological and Behavioral Abnormalities in a Mouse Model of CLN8-Batten DiseaseTyler B Johnson, Katherine A White, Jon J Brudvig, et al.Thyroid : Official Journal of the American Thyroid Association|March 30, 2022
AAV9-MCT8 Delivery at Juvenile Stage Ameliorates Neurological and Behavioral Deficits in a Mouse Model of MCT8-DeficiencyXiao-Hui Liao, Pablo Avalos, Oksana Shelest, et al.Proceedings of the National Academy of Sciences of the United States of America|October 1, 2016
Oligodendrocytes contribute to motor neuron death in ALS via SOD1-dependent mechanismLaura Ferraiuolo, Kathrin Meyer, Thomas W Sherwood, et al.Proceedings of the National Academy of Sciences of the United States of America|January 1, 2014
Direct conversion of patient fibroblasts demonstrates non-cell autonomous toxicity of astrocytes to motor neurons in familial and sporadic ALSKathrin Meyer, Laura Ferraiuolo, Carlos J Miranda, et al.Cell Reports|December 8, 2022
Mechanisms of IRF2BPL-related disorders and identification of a potential therapeutic strategyShrestha Sinha Ray, Debdeep Dutta, Cassandra Dennys, et al.Molecular Therapy. Methods & Clinical Development|March 5, 2021
Intracranial delivery of AAV9 gene therapy partially prevents retinal degeneration and visual deficits in CLN6-Batten disease miceKatherine A White, Hemanth R Nelvagal, Timothy A Poole, et al.Pageof 3