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Orphanet Journal of Rare Diseases
|
June 15, 2019
Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance
Mehmet Umut Akyol, Tord D Alden, Hernan Amartino, et al.
Orphanet Journal of Rare Diseases
|
May 31, 2019
Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance
Mehmet Umut Akyol, Tord D Alden, Hernan Amartino, et al.
Frontiers in Medicine
|
May 25, 2026
RNA activation as a precision dosing modality: MTL-CEBPA for controlled enzyme elevation in MPS I-H
Vikash Reebye, Konstantina Skourti-Stathaki, Konstantinos Vanezis, et al.
American Journal of Human Genetics
|
October 4, 2016
Recurrent De Novo Dominant Mutations in SLC25A4 Cause Severe Early-Onset Mitochondrial Disease and Loss of Mitochondrial DNA Copy Number
Kyle Thompson, Homa Majd, Cristina Dallabona, et al.
Science Signaling
|
November 30, 2017
Networks of enzymatically oxidized membrane lipids support calcium-dependent coagulation factor binding to maintain hemostasis
Sarah N Lauder, Keith Allen-Redpath, David A Slatter, et al.
Immunity
|
January 14, 2014
Interleukin-6 signaling drives fibrosis in unresolved inflammation
Ceri A Fielding, Gareth W Jones, Rachel M McLoughlin, et al.
Annals of Clinical and Translational Neurology
|
March 27, 2019
Leigh syndrome caused by mutations in <i>MTFMT</i> is associated with a better prognosis
Hannah Hayhurst, Irenaeus F M de Coo, Dorota Piekutowska-Abramczuk, et al.
Neurology
|
June 27, 2025
Metachromatic Leukodystrophy: New Therapy Advancements and Emerging Research Directions
Marije A B C Asbreuk, Daphne H Schoenmakers, Laura Ann Adang, et al.
The New England Journal of Medicine
|
November 17, 2021
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
Bernhard Gentner, Francesca Tucci, Stefania Galimberti, et al.
Page
of 26
Search research articles
Search
Showing results (251-260 of 259) with videos related to
Sort By:
Page
of 26
You have reached the last page of results.
This site can display upto 259 results.
Orphanet Journal of Rare Diseases
|
June 15, 2019
Recommendations for the management of MPS IVA: systematic evidence- and consensus-based guidance
Mehmet Umut Akyol, Tord D Alden, Hernan Amartino, et al.
Orphanet Journal of Rare Diseases
|
May 31, 2019
Recommendations for the management of MPS VI: systematic evidence- and consensus-based guidance
Mehmet Umut Akyol, Tord D Alden, Hernan Amartino, et al.
Frontiers in Medicine
|
May 25, 2026
RNA activation as a precision dosing modality: MTL-CEBPA for controlled enzyme elevation in MPS I-H
Vikash Reebye, Konstantina Skourti-Stathaki, Konstantinos Vanezis, et al.
American Journal of Human Genetics
|
October 4, 2016
Recurrent De Novo Dominant Mutations in SLC25A4 Cause Severe Early-Onset Mitochondrial Disease and Loss of Mitochondrial DNA Copy Number
Kyle Thompson, Homa Majd, Cristina Dallabona, et al.
Science Signaling
|
November 30, 2017
Networks of enzymatically oxidized membrane lipids support calcium-dependent coagulation factor binding to maintain hemostasis
Sarah N Lauder, Keith Allen-Redpath, David A Slatter, et al.
Immunity
|
January 14, 2014
Interleukin-6 signaling drives fibrosis in unresolved inflammation
Ceri A Fielding, Gareth W Jones, Rachel M McLoughlin, et al.
Annals of Clinical and Translational Neurology
|
March 27, 2019
Leigh syndrome caused by mutations in <i>MTFMT</i> is associated with a better prognosis
Hannah Hayhurst, Irenaeus F M de Coo, Dorota Piekutowska-Abramczuk, et al.
Neurology
|
June 27, 2025
Metachromatic Leukodystrophy: New Therapy Advancements and Emerging Research Directions
Marije A B C Asbreuk, Daphne H Schoenmakers, Laura Ann Adang, et al.
The New England Journal of Medicine
|
November 17, 2021
Hematopoietic Stem- and Progenitor-Cell Gene Therapy for Hurler Syndrome
Bernhard Gentner, Francesca Tucci, Stefania Galimberti, et al.
Page
of 26