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Child Neurology Open
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January 25, 2021
Classifying Hypomyelination: A Critical (White) Matter
Stefanie Perrier, Sara Matovic, Geneviève Bernard
Handbook of Clinical Neurology
|
September 25, 2024
Inherited white matter disorders: Hypomyelination (myelin disorders)
Stefanie Perrier, Laurence Gauquelin, Geneviève Bernard
Frontiers in Cellular Neuroscience
|
February 26, 2021
POLR3-Related Leukodystrophy: Exploring Potential Therapeutic Approaches
Stefanie Perrier, Mackenzie A Michell-Robinson, Geneviève Bernard
American Journal of Medical Genetics. Part A
|
November 13, 2021
Distinguishing severe phenotypes associated with pathogenic variants in POLR3A
Stefanie Perrier, Laurence Gauquelin, Jennifer A Wambach, et al.
NPJ Genomic Medicine
|
November 28, 2025
A scoping review of stem cell models of leukodystrophies: advances in understanding pathophysiological mechanisms
Alexandra Chapleau, Stefanie Perrier, Thomas M Durcan, et al.
Neurology
|
February 22, 2022
Oculodentodigital Dysplasia: A Cause of Hypomyelinating Leukodystrophy in Adults
Mackenzie A Michell-Robinson, Stefanie Perrier, Cassandra Lucia, et al.
International Journal of Radiation Oncology, Biology, Physics
|
February 10, 2022
Protection From Radiation-Induced Neuroanatomic Deficits by CCL2 Deficiency Is Dependent on Sex
A Elizabeth de Guzman, Mashal Ahmed, Stefanie Perrier, et al.
Orphanet Journal of Rare Diseases
|
July 13, 2023
Hypomyelination caused by a novel homozygous pathogenic variant in FOLR1: complete clinical and radiological recovery with oral folinic acid therapy and review of the literature
Ana Potic, Stefanie Perrier, Tijana Radovic, et al.
Frontiers in Neurology
|
November 2, 2023
Biallelic pathogenic variants in <i>POLR3D</i> alter tRNA transcription and cause a hypomyelinating leukodystrophy: A case report
Julia Macintosh, Stefanie Perrier, Maxime Pinard, et al.
Human Mutation
|
April 14, 2025
Novel Pathogenic Variants in <i>POLR3K</i> Cause POLR3-Related Leukodystrophy
Stefanie Perrier, Julia Macintosh, Agata D Misiaszek, et al.
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of 2
Search research articles
Search
Showing results (1-10 of 15) with videos related to
Sort By:
Page
of 2
Child Neurology Open
|
January 25, 2021
Classifying Hypomyelination: A Critical (White) Matter
Stefanie Perrier, Sara Matovic, Geneviève Bernard
Handbook of Clinical Neurology
|
September 25, 2024
Inherited white matter disorders: Hypomyelination (myelin disorders)
Stefanie Perrier, Laurence Gauquelin, Geneviève Bernard
Frontiers in Cellular Neuroscience
|
February 26, 2021
POLR3-Related Leukodystrophy: Exploring Potential Therapeutic Approaches
Stefanie Perrier, Mackenzie A Michell-Robinson, Geneviève Bernard
American Journal of Medical Genetics. Part A
|
November 13, 2021
Distinguishing severe phenotypes associated with pathogenic variants in POLR3A
Stefanie Perrier, Laurence Gauquelin, Jennifer A Wambach, et al.
NPJ Genomic Medicine
|
November 28, 2025
A scoping review of stem cell models of leukodystrophies: advances in understanding pathophysiological mechanisms
Alexandra Chapleau, Stefanie Perrier, Thomas M Durcan, et al.
Neurology
|
February 22, 2022
Oculodentodigital Dysplasia: A Cause of Hypomyelinating Leukodystrophy in Adults
Mackenzie A Michell-Robinson, Stefanie Perrier, Cassandra Lucia, et al.
International Journal of Radiation Oncology, Biology, Physics
|
February 10, 2022
Protection From Radiation-Induced Neuroanatomic Deficits by CCL2 Deficiency Is Dependent on Sex
A Elizabeth de Guzman, Mashal Ahmed, Stefanie Perrier, et al.
Orphanet Journal of Rare Diseases
|
July 13, 2023
Hypomyelination caused by a novel homozygous pathogenic variant in FOLR1: complete clinical and radiological recovery with oral folinic acid therapy and review of the literature
Ana Potic, Stefanie Perrier, Tijana Radovic, et al.
Frontiers in Neurology
|
November 2, 2023
Biallelic pathogenic variants in <i>POLR3D</i> alter tRNA transcription and cause a hypomyelinating leukodystrophy: A case report
Julia Macintosh, Stefanie Perrier, Maxime Pinard, et al.
Human Mutation
|
April 14, 2025
Novel Pathogenic Variants in <i>POLR3K</i> Cause POLR3-Related Leukodystrophy
Stefanie Perrier, Julia Macintosh, Agata D Misiaszek, et al.
Page
of 2