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Human Gene Therapy|December 2, 2016
A 5' Noncoding Exon Containing Engineered Intron Enhances Transgene Expression from Recombinant AAV Vectors in vivoJiamiao Lu, James A Williams, Jeremy Luke, et al.Nature Genetics|June 5, 2003
AAV serotype 2 vectors preferentially integrate into active genes in miceHiroyuki Nakai, Eugenio Montini, Sally Fuess, et al.Disease Models & Mechanisms|December 17, 2020
Disruption of a hedgehog-foxf1-rspo2 signaling axis leads to tracheomalacia and a loss of sox9+ tracheal chondrocytesTalia Nasr, Andrea M Holderbaum, Praneet Chaturvedi, et al.Nature Biotechnology|September 24, 2002
Transposition from a gutless adeno-transposon vector stabilizes transgene expression in vivoStephen R Yant, Anja Ehrhardt, Jacob Giehm Mikkelsen, et al.Hepatology (Baltimore, Md.)|February 18, 2010
Adeno-associated virus gene repair corrects a mouse model of hereditary tyrosinemia in vivoNicole K Paulk, Karsten Wursthorn, Zhongya Wang, et al.Nature Protocols|April 18, 2009
A rapid protocol for construction and production of high-capacity adenoviral vectorsLorenz Jager, Martin A Hausl, Christina Rauschhuber, et al.Journal of Virology|December 15, 2004
Unrestricted hepatocyte transduction with adeno-associated virus serotype 8 vectors in miceHiroyuki Nakai, Sally Fuess, Theresa A Storm, et al.Molecular and Cellular Biology|March 4, 2005
High-resolution genome-wide mapping of transposon integration in mammalsStephen R Yant, Xiaolin Wu, Yong Huang, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|October 8, 2003
Helper-Independent Sleeping Beauty transposon-transposase vectors for efficient nonviral gene delivery and persistent gene expression in vivoJacob Giehm Mikkelsen, Stephen R Yant, Leonard Meuse, et al.Molecular Therapy : the Journal of the American Society of Gene Therapy|September 20, 2012
Ribosomal DNA integrating rAAV-rDNA vectors allow for stable transgene expressionLeszek Lisowski, Ashley Lau, Zhongya Wang, et al.Pageof 19